Monogenic causes of chronic kidney disease in adults.


Journal

Kidney international
ISSN: 1523-1755
Titre abrégé: Kidney Int
Pays: United States
ID NLM: 0323470

Informations de publication

Date de publication:
04 2019
Historique:
received: 29 05 2018
revised: 10 10 2018
accepted: 19 10 2018
pubmed: 19 2 2019
medline: 15 2 2020
entrez: 19 2 2019
Statut: ppublish

Résumé

Approximately 500 monogenic causes of chronic kidney disease (CKD) have been identified, mainly in pediatric populations. The frequency of monogenic causes among adults with CKD has been less extensively studied. To determine the likelihood of detecting monogenic causes of CKD in adults presenting to nephrology services in Ireland, we conducted whole exome sequencing (WES) in a multi-centre cohort of 114 families including 138 affected individuals with CKD. Affected adults were recruited from 78 families with a positive family history, 16 families with extra-renal features, and 20 families with neither a family history nor extra-renal features. We detected a pathogenic mutation in a known CKD gene in 42 of 114 families (37%). A monogenic cause was identified in 36% of affected families with a positive family history of CKD, 69% of those with extra-renal features, and only 15% of those without a family history or extra-renal features. There was no difference in the rate of genetic diagnosis in individuals with childhood versus adult onset CKD. Among the 42 families in whom a monogenic cause was identified, WES confirmed the clinical diagnosis in 17 (40%), corrected the clinical diagnosis in 9 (22%), and established a diagnosis for the first time in 16 families referred with CKD of unknown etiology (38%). In this multi-centre study of adults with CKD, a molecular genetic diagnosis was established in over one-third of families. In the evolving era of precision medicine, WES may be an important tool to identify the cause of CKD in adults.

Identifiants

pubmed: 30773290
pii: S0085-2538(18)30839-1
doi: 10.1016/j.kint.2018.10.031
pmc: PMC6431580
mid: NIHMS1516136
pii:
doi:

Types de publication

Evaluation Study Journal Article Multicenter Study Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

914-928

Subventions

Organisme : NIDDK NIH HHS
ID : R01 DK088767
Pays : United States
Organisme : NIDDK NIH HHS
ID : P30 DK079310
Pays : United States
Organisme : NIH HHS
ID : S10 OD018521
Pays : United States
Organisme : NIDDK NIH HHS
ID : R01 DK076683
Pays : United States
Organisme : NCI NIH HHS
ID : T32 CA009172
Pays : United States
Organisme : NHGRI NIH HHS
ID : U54 HG006504
Pays : United States
Organisme : NIDDK NIH HHS
ID : R01 DK068306
Pays : United States
Organisme : NIDDK NIH HHS
ID : T32 DK007726
Pays : United States

Commentaires et corrections

Type : CommentIn

Informations de copyright

Copyright © 2019 International Society of Nephrology. Published by Elsevier Inc. All rights reserved.

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Auteurs

Dervla M Connaughton (DM)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA; Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland; Trinity Health Kidney Centre, Trinity Translational Medicine Institute, Trinity College Dublin, Dublin, Ireland.

Claire Kennedy (C)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland.

Shirlee Shril (S)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Nina Mann (N)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Susan L Murray (SL)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland.

Patrick A Williams (PA)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland; Royal College of Surgeons in Ireland, Dublin, Ireland.

Eoin Conlon (E)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland; Royal College of Surgeons in Ireland, Dublin, Ireland.

Makiko Nakayama (M)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Amelie T van der Ven (AT)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Hadas Ityel (H)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Franziska Kause (F)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Caroline M Kolvenbach (CM)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Rufeng Dai (R)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Asaf Vivante (A)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA; Sackler Faculty of Medicine, Tel Aviv University, Tel Aviv, Israel.

Daniela A Braun (DA)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Ronen Schneider (R)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Thomas M Kitzler (TM)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA.

Brona Moloney (B)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland.

Conor P Moran (CP)

Department of Nephrology, Belfast-Ulster Hospital, Belfast, Northern Ireland.

John S Smyth (JS)

Department of Nephrology, Belfast-Ulster Hospital, Belfast, Northern Ireland.

Alan Kennedy (A)

Trinity Health Kidney Centre, Trinity Translational Medicine Institute, Trinity College Dublin, Dublin, Ireland.

Katherine Benson (K)

Royal College of Surgeons in Ireland, Dublin, Ireland.

Caragh Stapleton (C)

Royal College of Surgeons in Ireland, Dublin, Ireland.

Mark Denton (M)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland.

Colm Magee (C)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland.

Conall M O'Seaghdha (CM)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland.

William D Plant (WD)

Department of Renal Medicine, Cork University Hospital and University College Cork, Cork, Ireland.

Matthew D Griffin (MD)

Department of Nephrology, Galway University Hospital and School of Medicine, National University of Ireland, Galway, Ireland.

Atif Awan (A)

National Paediatric Haemodialysis Centre and Renal Transplant Unit, Temple Street Children's University Hospital, Dublin, Ireland.

Clodagh Sweeney (C)

National Paediatric Haemodialysis Centre and Renal Transplant Unit, Temple Street Children's University Hospital, Dublin, Ireland.

Shrikant M Mane (SM)

Department of Genetics, Yale University School of Medicine, New Haven, Connecticut, USA.

Richard P Lifton (RP)

Department of Genetics, Yale University School of Medicine, New Haven, Connecticut, USA; Rockefeller University, New York, New York, USA.

Brenda Griffin (B)

Trinity Health Kidney Centre, Trinity Translational Medicine Institute, Trinity College Dublin, Dublin, Ireland.

Sean Leavey (S)

Department of Nephrology, University Hospital Waterford, Waterford, Ireland.

Liam Casserly (L)

Departments of Nephrology and Internal Medicine, University Hospital Limerick, Limerick, Ireland.

Declan G de Freitas (DG)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland.

John Holian (J)

Department of Nephrology, St. Vincent's University Hospital, Dublin, Ireland.

Anthony Dorman (A)

Royal College of Surgeons in Ireland, Dublin, Ireland; Department of Histopathology, Beaumont Hospital, Dublin, Ireland.

Brendan Doyle (B)

Department of Histopathology, Beaumont Hospital, Dublin, Ireland.

Peter J Lavin (PJ)

Trinity Health Kidney Centre, Trinity College Dublin, Tallaght University Hospital, Dublin, Ireland.

Mark A Little (MA)

Trinity Health Kidney Centre, Trinity Translational Medicine Institute, Trinity College Dublin, Dublin, Ireland.

Peter J Conlon (PJ)

Department of Nephrology & Transplantation, Beaumont Hospital, Dublin, Ireland; Royal College of Surgeons in Ireland, Dublin, Ireland. Electronic address: peterconlon@beaumont.ie.

Friedhelm Hildebrandt (F)

Department of Medicine, Boston Children's Hospital, Harvard Medical School, Boston, Massachusetts, USA. Electronic address: friedhelm.hildebrandt@childrens.harvard.edu.

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