Androgenetic chimerism as an etiology for Beckwith-Wiedemann syndrome: diagnosis and management.


Journal

Genetics in medicine : official journal of the American College of Medical Genetics
ISSN: 1530-0366
Titre abrégé: Genet Med
Pays: United States
ID NLM: 9815831

Informations de publication

Date de publication:
11 2019
Historique:
received: 22 01 2019
accepted: 14 05 2019
pubmed: 31 5 2019
medline: 28 4 2020
entrez: 1 6 2019
Statut: ppublish

Résumé

Beckwith-Wiedemann syndrome (BWS) is a human genomic imprinting disorder characterized by lateralized overgrowth, macroglossia, abdominal wall defects, congenital hyperinsulinism, and predisposition to embryonal tumors. One of the molecular etiologies underlying BWS is paternal uniparental isodisomy of chromosome 11p15.5 (pUPD11). About 8% of pUPD11 cases are due to genome-wide paternal uniparental isodisomy (GWpUPD). About 30 cases of live-born patients with GWpUPD have been described, most of whom were mosaic and female. We present male patients with BWS due to GWpUPD, elucidate the underlying mechanism, and make recommendations for management. Three male patients with GWpUPD underwent clinical and molecular evaluation by single-nucleotide polymorphism (SNP) microarrays in different tissues. Previously published cases of GWpUPD were reviewed. SNP microarray demonstrated a GWpUPD cell population with sex chromosomes XX and biparental cell population with sex chromosomes XY, consistent with dispermic androgenetic chimerism. SNP microarray is necessary to distinguish GWpUPD cases and the underlying mechanisms. The percentage of GWpUPD cell population within a specific tissue type correlated with the amount of tissue dysplasia. Males with BWS due to GWpUPD are important to distinguish from other molecular etiologies because the mechanism indicates risk for germ cell tumors and autosomal recessive diseases in addition to other BWS features.

Identifiants

pubmed: 31147633
doi: 10.1038/s41436-019-0551-9
pii: S1098-3600(21)01075-3
pmc: PMC7848850
mid: NIHMS1663425
doi:

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

2644-2649

Subventions

Organisme : NCI NIH HHS
ID : K08 CA193915
Pays : United States

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Auteurs

Sarah E Sheppard (SE)

Division of Human Genetics, Children's Hospital of Philadelphia, Philadelphia, PA, USA.

Emilie Lalonde (E)

Department of Pathology and Laboratory Medicine, Children's Hospital of Philadelphia, Philadelphia, PA, USA.
Department of Pathology and Laboratory Medicine, University of Pennsylvania Health System, Philadelphia, PA, USA.

N Scott Adzick (NS)

Department of Surgery, Children's Hospital of Philadelphia, Philadelphia, PA, USA.

Anita E Beck (AE)

Department of Pediatrics, Division of Genetic Medicine, University of Washington & Seattle Children's Hospital, Seattle, WA, USA.

Tricia Bhatti (T)

Department of Pathology and Laboratory Medicine, Children's Hospital of Philadelphia, Philadelphia, PA, USA.

Diva D De Leon (DD)

Division of Endocrinology and Diabetes, The Children's Hospital of Philadelphia, Philadelphia, PA, USA.
Department of Pediatrics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.

Kelly A Duffy (KA)

Division of Human Genetics, Children's Hospital of Philadelphia, Philadelphia, PA, USA.

Arupa Ganguly (A)

Department of Pathology and Laboratory Medicine, University of Pennsylvania Health System, Philadelphia, PA, USA.
Department of Genetics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.

Evan Hathaway (E)

Division of Human Genetics, Children's Hospital of Philadelphia, Philadelphia, PA, USA.

Jianling Ji (J)

Center for Personalized Medicine, Department of Pathology & Laboratory Medicine, Children's Hospital Los Angeles, and Department of Pathology, Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.

Rebecca Linn (R)

Department of Pathology and Laboratory Medicine, Children's Hospital of Philadelphia, Philadelphia, PA, USA.

Katherine Lord (K)

Division of Endocrinology and Diabetes, The Children's Hospital of Philadelphia, Philadelphia, PA, USA.
Department of Pediatrics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA.

Linda M Randolph (LM)

Division of Medical Genetics, Department of Pediatrics, Children's Hospital Los Angeles and Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.

Brian Sajorda (B)

Division of Human Genetics, Children's Hospital of Philadelphia, Philadelphia, PA, USA.

Lisa States (L)

Department of Radiology, Children's Hospital of Philadelphia, Philadelphia, PA, USA.

Laura K Conlin (LK)

Department of Pathology and Laboratory Medicine, Children's Hospital of Philadelphia, Philadelphia, PA, USA.

Jennifer M Kalish (JM)

Division of Human Genetics, Children's Hospital of Philadelphia, Philadelphia, PA, USA. Kalishj@email.chop.edu.
Department of Pediatrics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. Kalishj@email.chop.edu.
Department of Genetics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. Kalishj@email.chop.edu.

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Classifications MeSH