Proteomic Analysis in Morquio A Cells Treated with Immobilized Enzymatic Replacement Therapy on Nanostructured Lipid Systems.
enzyme replacement therapy
lysosomal disorders
nanoparticles
proteomics
Journal
International journal of molecular sciences
ISSN: 1422-0067
Titre abrégé: Int J Mol Sci
Pays: Switzerland
ID NLM: 101092791
Informations de publication
Date de publication:
18 Sep 2019
18 Sep 2019
Historique:
received:
22
08
2019
revised:
07
09
2019
accepted:
13
09
2019
entrez:
22
9
2019
pubmed:
22
9
2019
medline:
8
2
2020
Statut:
epublish
Résumé
Morquio A syndrome, or mucopolysaccharidosis type IVA (MPS IVA), is a lysosomal storage disease due to mutations in the N-acetylgalactosamine-6-sulfatase (
Identifiants
pubmed: 31540344
pii: ijms20184610
doi: 10.3390/ijms20184610
pmc: PMC6769449
pii:
doi:
Substances chimiques
Lipids
0
Liposomes
0
Chondroitinsulfatases
EC 3.1.6.-
GALNS protein, human
EC 3.1.6.4
Types de publication
Journal Article
Langues
eng
Sous-ensembles de citation
IM
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