Inhibition of the transcription factor ROR-γ reduces pathogenic Th17 cells in acetylcholine receptor antibody positive myasthenia gravis.


Journal

Experimental neurology
ISSN: 1090-2430
Titre abrégé: Exp Neurol
Pays: United States
ID NLM: 0370712

Informations de publication

Date de publication:
03 2020
Historique:
received: 12 08 2019
revised: 27 11 2019
accepted: 10 12 2019
pubmed: 16 12 2019
medline: 24 10 2020
entrez: 16 12 2019
Statut: ppublish

Résumé

IL-17 producing CD4 T cells (Th17) cells increase significantly with disease severity in myasthenia gravis (MG) patients. To suppress the generation of Th17 cells, we examined the effect of inhibiting retinoic acid receptor-related-orphan-receptor-C (RORγ), a Th17-specific transcription factor critical for differentiation. RORγ inhibition profoundly reduced Th17 cell frequencies, including IFN-γ and IL-17 co-producing pathogenic Th17 cells. Other T helper subsets were not affected. In parallel, CD8 T cell subsets producing IL-17 and IL-17/IFN-γ were increased in MG patients and inhibited by the RORγ inhibitor. These findings provide rationale for exploration of targeted Th17 therapies, including ROR-γ inhibitors, to treat MG patients.

Identifiants

pubmed: 31838097
pii: S0014-4886(19)30293-6
doi: 10.1016/j.expneurol.2019.113146
pmc: PMC7357824
mid: NIHMS1599249
pii:
doi:

Substances chimiques

Autoantibodies 0
Autoantigens 0
IL17A protein, human 0
Immunologic Factors 0
Interleukin-17 0
Nuclear Receptor Subfamily 1, Group F, Member 3 0
Receptors, Cholinergic 0

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

113146

Subventions

Organisme : NINDS NIH HHS
ID : K23 NS085049
Pays : United States

Informations de copyright

Copyright © 2019 Elsevier Inc. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of Competing Interest The authors declare that they have no conflicts of interest.

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Auteurs

John S Yi (JS)

Division of Surgical Sciences, Department of Surgery, Duke University Medical Center, 915 S., LaSalle Street, Box 2926, Durham, NC 27710, USA. Electronic address: john.yi@duke.edu.

Melissa A Russo (MA)

Neuromuscular Section, Department of Neurology, Duke University Medical Center, Box 3403, Durham, NC 27710, USA.

Shruti Raja (S)

Neuromuscular Section, Department of Neurology, Duke University Medical Center, Box 3403, Durham, NC 27710, USA.

Janice M Massey (JM)

Neuromuscular Section, Department of Neurology, Duke University Medical Center, Box 3403, Durham, NC 27710, USA.

Vern C Juel (VC)

Neuromuscular Section, Department of Neurology, Duke University Medical Center, Box 3403, Durham, NC 27710, USA.

Jay Shin (J)

Duke University, Durham, NC 27710, USA.

Lisa D Hobson-Webb (LD)

Neuromuscular Section, Department of Neurology, Duke University Medical Center, Box 3403, Durham, NC 27710, USA.

Karissa Gable (K)

Neuromuscular Section, Department of Neurology, Duke University Medical Center, Box 3403, Durham, NC 27710, USA.

Jeffrey T Guptill (JT)

Neuromuscular Section, Department of Neurology, Duke University Medical Center, Box 3403, Durham, NC 27710, USA.

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