[Analysis of DPYS gene variants in a child with dihydropyrimidase deficiency].


Journal

Zhonghua yi xue yi chuan xue za zhi = Zhonghua yixue yichuanxue zazhi = Chinese journal of medical genetics
ISSN: 1003-9406
Titre abrégé: Zhonghua Yi Xue Yi Chuan Xue Za Zhi
Pays: China
ID NLM: 9425197

Informations de publication

Date de publication:
10 Jun 2020
Historique:
entrez: 31 5 2020
pubmed: 31 5 2020
medline: 24 10 2020
Statut: ppublish

Résumé

To explore the genetic basis for a child with dihydropyrimidase (DHP) deficiency. High-throughput sequencing was carried out for the child. Suspected variants were verified by using Sanger sequencing. The proband was found to carry compound heterozygous variants of the DPYS gene, namely c.1468C>T (a missense variant) and c.1339-1363del (a frameshifting variant). The compound heterozygous variants of the DPYS gene probably underlie the DHP in this child. Above result has enabled genetic counseling and prenatal diagnosis for his parents.

Identifiants

pubmed: 32472544
pii: 940637133
doi: 10.3760/cma.j.issn.1003-9406.2020.06.013
doi:

Substances chimiques

Nerve Tissue Proteins 0

Types de publication

Journal Article

Langues

chi

Sous-ensembles de citation

IM

Pagination

650-652

Auteurs

Meifang Lei (M)

Department of Neurology, Tianjin Pediatric Hospital, Tianjin 300074, China. zhangyuqin0809@sina.com.

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Classifications MeSH