CSNK2B: A broad spectrum of neurodevelopmental disability and epilepsy severity.


Journal

Epilepsia
ISSN: 1528-1167
Titre abrégé: Epilepsia
Pays: United States
ID NLM: 2983306R

Informations de publication

Date de publication:
07 2021
Historique:
revised: 30 04 2021
received: 17 12 2020
accepted: 03 05 2021
pubmed: 28 5 2021
medline: 16 10 2021
entrez: 27 5 2021
Statut: ppublish

Résumé

CSNK2B has recently been implicated as a disease gene for neurodevelopmental disability (NDD) and epilepsy. Information about developmental outcomes has been limited by the young age and short follow-up for many of the previously reported cases, and further delineation of the spectrum of associated phenotypes is needed. We present 25 new patients with variants in CSNK2B and refine the associated NDD and epilepsy phenotypes. CSNK2B variants were identified by research or clinical exome sequencing, and investigators from different centers were connected via GeneMatcher. Most individuals had developmental delay and generalized epilepsy with onset in the first 2 years. However, we found a broad spectrum of phenotypic severity, ranging from early normal development with pharmacoresponsive seizures to profound intellectual disability with intractable epilepsy and recurrent refractory status epilepticus. These findings suggest that CSNK2B should be considered in the diagnostic evaluation of patients with a broad range of NDD with treatable or intractable seizures.

Identifiants

pubmed: 34041744
doi: 10.1111/epi.16931
pmc: PMC9189716
mid: NIHMS1809891
doi:

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

e103-e109

Subventions

Organisme : NICHD NIH HHS
ID : P50 HD105351
Pays : United States
Organisme : NCATS NIH HHS
ID : UL1 TR001873
Pays : United States
Organisme : NHGRI NIH HHS
ID : UM1 HG008900
Pays : United States

Informations de copyright

© 2021 International League Against Epilepsy.

Références

Biochem Biophys Res Commun. 2004 Sep 17;322(2):542-50
pubmed: 15325264
Nature. 2020 May;581(7809):434-443
pubmed: 32461654
Mol Cell Biochem. 2011 Oct;356(1-2):169-75
pubmed: 21761202
Hum Mutat. 2017 Aug;38(8):932-941
pubmed: 28585349
J Hum Genet. 2019 Apr;64(4):313-322
pubmed: 30655572
Proc Natl Acad Sci U S A. 1991 Nov 15;88(22):10232-6
pubmed: 1946443
Epilepsia. 2017 Apr;58(4):512-521
pubmed: 28276062
Cell Death Differ. 2018 Jan;25(1):154-160
pubmed: 29099487
J Physiol. 2008 Jul 1;586(13):3195-206
pubmed: 18483072
Hum Mutat. 2015 Oct;36(10):928-30
pubmed: 26220891
Cell Mol Life Sci. 2009 Jun;66(11-12):1817-29
pubmed: 19387552
Hum Genet. 2016 Jul;135(7):699-705
pubmed: 27048600
EMBO J. 1993 Apr;12(4):1633-40
pubmed: 8467810
Hum Mutat. 2017 Nov;38(11):1611-1612
pubmed: 28762608
Genet Med. 2015 May;17(5):405-24
pubmed: 25741868
Sci Rep. 2019 Nov 29;9(1):17909
pubmed: 31784560
Acta Anat (Basel). 1994;149(1):13-20
pubmed: 8184654
J Biol Chem. 1995 Jun 2;270(22):13017-21
pubmed: 7768894

Auteurs

Michelle E Ernst (ME)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.
Department of Genetics and Development, Columbia University Irving Medical Center, New York, NY, USA.

Evan H Baugh (EH)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Amanda Thomas (A)

Department of Pathology and Cell Biology, Columbia University Irving Medical Center, New York, NY, USA.

Louise Bier (L)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Natalie Lippa (N)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Nicholas Stong (N)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Maureen S Mulhern (MS)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Sulagna Kushary (S)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Cigdem I Akman (CI)

Department of Neurology, The Neurological Institute of New York, Columbia University Irving Medical Center, New York, NY, USA.

Erin L Heinzen (EL)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.
Eshelman School of Pharmacy, University of North Carolina at Chapel Hill, Chapel Hill, NC, USA.

Raymond Yeh (R)

Department of Pathology and Cell Biology, Columbia University Irving Medical Center, New York, NY, USA.

Weimin Bi (W)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, USA.

Neil A Hanchard (NA)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, USA.

Lindsay C Burrage (LC)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, USA.

Magalie S Leduc (MS)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, TX, USA.

Josephine S C Chong (JSC)

Joint CUHK-Baylor Center of Medical Genetics, Faculty of Medicine, The Chinese University of Hong Kong, Hong Kong SAR, China.

Renee Bend (R)

Greenwood Genetic Center, Greenwood, SC, USA.

Michael J Lyons (MJ)

Greenwood Genetic Center, Greenwood, SC, USA.

Jennifer A Lee (JA)

Greenwood Genetic Center, Greenwood, SC, USA.

Pim Suwannarat (P)

Mid-Atlantic Permanente Medical Group, Rockville, MD, USA.

Eva Brilstra (E)

Department of Genetics, University Medical Center Utrecht, Utrecht, The Netherlands.

Marleen Simon (M)

Department of Genetics, University Medical Center Utrecht, Utrecht, The Netherlands.

Marije Koopmans (M)

Department of Genetics, University Medical Center Utrecht, Utrecht, The Netherlands.

Ellen van Binsbergen (E)

Department of Genetics, University Medical Center Utrecht, Utrecht, The Netherlands.

Daniel Groepper (D)

Department of Pediatrics, Southern Illinois University School of Medicine, Springfield, IL, USA.

Julie Fleischer (J)

Department of Pediatrics, Southern Illinois University School of Medicine, Springfield, IL, USA.

Caroline Nava (C)

Department of Genetics, APHP Sorbonne University, Paris, France.

Boris Keren (B)

Department of Genetics, APHP Sorbonne University, Paris, France.

Cyril Mignot (C)

Department of Genetics, APHP Sorbonne University, Paris, France.
Reference Center for Intellectual Disabilities of Rare Causes, Paris, France.

Sophie Mathieu (S)

Department of Neuropediatrics, APHP Sorbonne University, Trousseau Hospital, Paris, France.

Grazia M S Mancini (GMS)

Department of Clinical Genetics, ErasmusMC University Medical Center, Rotterdam, The Netherlands.

Suneeta Madan-Khetarpal (S)

Department of Medical Genetics, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

Elena M Infante (EM)

Department of Medical Genetics, UPMC Children's Hospital of Pittsburgh, Pittsburgh, PA, USA.

Judith Bluvstein (J)

School of Medicine, New York University, New York, NY, USA.

Andrea Seeley (A)

Geisinger Medical Center, Danville, PA, USA.

Kristine Bachman (K)

Geisinger Medical Center, Danville, PA, USA.

Eric W Klee (EW)

Center for Individualized Medicine, Mayo Clinic, Rochester, MN, USA.
Department of Health Sciences, Mayo Clinic, Rochester, MN, USA.

Laura E Schultz-Rogers (LE)

Center for Individualized Medicine, Mayo Clinic, Rochester, MN, USA.
Department of Health Sciences, Mayo Clinic, Rochester, MN, USA.

Linda Hasadsri (L)

Division of Laboratory Genetics and Genomics, Department of Laboratory Medicine and Pathology, Mayo Clinic, Rochester, MN, USA.

Sarah Barnett (S)

Division of Laboratory Genetics and Genomics, Department of Laboratory Medicine and Pathology, Mayo Clinic, Rochester, MN, USA.

Marissa S Ellingson (MS)

Division of Laboratory Genetics and Genomics, Department of Laboratory Medicine and Pathology, Mayo Clinic, Rochester, MN, USA.

Matthew J Ferber (MJ)

Clinical Genome Sequencing Laboratory, Department of Laboratory Medicine and Pathology, Mayo Clinic, Rochester, MN, USA.

Vinodh Narayanan (V)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, AZ, USA.

Keri Ramsey (K)

Center for Rare Childhood Disorders, Translational Genomics Research Institute, Phoenix, AZ, USA.

Anita Rauch (A)

Institute of Medical Genetics, University of Zürich, Schlieren, Zürich, Switzerland.

Pascal Joset (P)

Institute of Medical Genetics, University of Zürich, Schlieren, Zürich, Switzerland.

Katharina Steindl (K)

Institute of Medical Genetics, University of Zürich, Schlieren, Zürich, Switzerland.

Theodore Sheehan (T)

Department of Neurology, Boston Children's Hospital, Boston, MA, USA.

Annapurna Poduri (A)

Department of Neurology, Boston Children's Hospital, Boston, MA, USA.

Alejandra Vasquez (A)

Department of Neurology, Boston Children's Hospital, Boston, MA, USA.
Division of Child and Adolescent Neurology, Department of Neurology, Mayo Clinic, Rochester, MN, USA.

Claudia Ruivenkamp (C)

Department of Clinical Genetics, Leiden University Medical Center (LUMC), Leiden, the Netherlands.

Susan M White (SM)

Victorian Clinical Genetics Service, Murdoch Children's Research Institute, Melbourne, Australia.
Department of Paediatrics, University of Melbourne, Melbourne, Australia.

Lynn Pais (L)

Center for Mendelian Genomics, Broad Institute of MIT and Harvard, Cambridge, MA, USA.

Kristin G Monaghan (KG)

GeneDx, Gaithersburg, MD, USA.

David B Goldstein (DB)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Tristan T Sands (TT)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.
Department of Neurology, The Neurological Institute of New York, Columbia University Irving Medical Center, New York, NY, USA.

Vimla Aggarwal (V)

Institute for Genomic Medicine, Columbia University Irving Medical Center, New York, NY, USA.
Department of Pathology and Cell Biology, Columbia University Irving Medical Center, New York, NY, USA.

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