Direct characterization of cis-regulatory elements and functional dissection of complex genetic associations using HCR-FlowFISH.


Journal

Nature genetics
ISSN: 1546-1718
Titre abrégé: Nat Genet
Pays: United States
ID NLM: 9216904

Informations de publication

Date de publication:
08 2021
Historique:
received: 27 05 2020
accepted: 23 06 2021
pubmed: 31 7 2021
medline: 11 9 2021
entrez: 30 7 2021
Statut: ppublish

Résumé

Effective interpretation of genome function and genetic variation requires a shift from epigenetic mapping of cis-regulatory elements (CREs) to characterization of endogenous function. We developed hybridization chain reaction fluorescence in situ hybridization coupled with flow cytometry (HCR-FlowFISH), a broadly applicable approach to characterize CRISPR-perturbed CREs via accurate quantification of native transcripts, alongside CRISPR activity screen analysis (CASA), a hierarchical Bayesian model to quantify CRE activity. Across >325,000 perturbations, we provide evidence that CREs can regulate multiple genes, skip over the nearest gene and display activating and/or silencing effects. At the cholesterol-level-associated FADS locus, we combine endogenous screens with reporter assays to exhaustively characterize multiple genome-wide association signals, functionally nominate causal variants and, importantly, identify their target genes.

Identifiants

pubmed: 34326544
doi: 10.1038/s41588-021-00900-4
pii: 10.1038/s41588-021-00900-4
pmc: PMC8925018
mid: NIHMS1723995
doi:

Substances chimiques

Adaptor Proteins, Signal Transducing 0
Delta-5 Fatty Acid Desaturase 0
GATA1 Transcription Factor 0
GATA1 protein, human 0
LIM Domain Proteins 0
LMO2 protein, human 0
Proto-Oncogene Proteins 0
RNA, Guide 0
Fatty Acid Desaturases EC 1.14.19.-
Deoxyribonuclease I EC 3.1.21.1

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1166-1176

Subventions

Organisme : NHGRI NIH HHS
ID : R00 HG008179
Pays : United States
Organisme : NIGMS NIH HHS
ID : T32 GM007226
Pays : United States
Organisme : Howard Hughes Medical Institute
Pays : United States
Organisme : NHGRI NIH HHS
ID : R00 HG010669
Pays : United States
Organisme : NHGRI NIH HHS
ID : K99 HG008179
Pays : United States
Organisme : NHGRI NIH HHS
ID : UM1 HG009435
Pays : United States
Organisme : NHGRI NIH HHS
ID : F32 HG009226
Pays : United States
Organisme : NHGRI NIH HHS
ID : K99 HG010669
Pays : United States
Organisme : NIAID NIH HHS
ID : R01 AI151051
Pays : United States

Commentaires et corrections

Type : ErratumIn

Informations de copyright

© 2021. The Author(s), under exclusive licence to Springer Nature America, Inc.

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Auteurs

Steven K Reilly (SK)

Broad Institute of MIT and Harvard, Cambridge, MA, USA. sreilly@broadinstitute.org.
Center for System Biology, Department of Organismic and Evolutionary Biology, Harvard University, Cambridge, MA, USA. sreilly@broadinstitute.org.

Sager J Gosai (SJ)

Broad Institute of MIT and Harvard, Cambridge, MA, USA.
Center for System Biology, Department of Organismic and Evolutionary Biology, Harvard University, Cambridge, MA, USA.
Harvard Graduate Program in Biological and Biomedical Science, Boston, MA, USA.

Alan Gutierrez (A)

Broad Institute of MIT and Harvard, Cambridge, MA, USA.

Ava Mackay-Smith (A)

Broad Institute of MIT and Harvard, Cambridge, MA, USA.

Jacob C Ulirsch (JC)

Broad Institute of MIT and Harvard, Cambridge, MA, USA.
Harvard Graduate Program in Biological and Biomedical Science, Boston, MA, USA.
Analytic and Translational Genetics Unit, Massachusetts General Hospital, Boston, MA, USA.

Masahiro Kanai (M)

Broad Institute of MIT and Harvard, Cambridge, MA, USA.
Analytic and Translational Genetics Unit, Massachusetts General Hospital, Boston, MA, USA.
Program in Bioinformatics and Integrative Genomics, Harvard Medical School, Boston, MA, USA.

Kousuke Mouri (K)

The Jackson Laboratory, Bar Harbor, ME, USA.

Daniel Berenzy (D)

The Jackson Laboratory, Bar Harbor, ME, USA.

Susan Kales (S)

The Jackson Laboratory, Bar Harbor, ME, USA.

Gina M Butler (GM)

Broad Institute of MIT and Harvard, Cambridge, MA, USA.

Adrianne Gladden-Young (A)

Broad Institute of MIT and Harvard, Cambridge, MA, USA.

Redwan M Bhuiyan (RM)

The Jackson Laboratory for Genomic Medicine, Farmington, CT, USA.
Department of Genetics and Genome Sciences, University of Connecticut, Farmington, CT, USA.

Michael L Stitzel (ML)

The Jackson Laboratory for Genomic Medicine, Farmington, CT, USA.
Department of Genetics and Genome Sciences, University of Connecticut, Farmington, CT, USA.
Institute of Systems Genomics, University of Connecticut, Farmington, CT, USA.

Hilary K Finucane (HK)

Broad Institute of MIT and Harvard, Cambridge, MA, USA.
Analytic and Translational Genetics Unit, Massachusetts General Hospital, Boston, MA, USA.

Pardis C Sabeti (PC)

Broad Institute of MIT and Harvard, Cambridge, MA, USA. pardis@broadinstitute.org.
Center for System Biology, Department of Organismic and Evolutionary Biology, Harvard University, Cambridge, MA, USA. pardis@broadinstitute.org.
Howard Hughes Medical Institute, Chevy Chase, MD, USA. pardis@broadinstitute.org.
Department of Immunology and Infectious Disease, Harvard T.H. Chan School of Public Health, Boston, MA, USA. pardis@broadinstitute.org.

Ryan Tewhey (R)

The Jackson Laboratory, Bar Harbor, ME, USA. ryan.tewhey@jax.org.
Graduate School of Biomedical Sciences and Engineering, University of Maine, Orono, ME, USA. ryan.tewhey@jax.org.
Graduate School of Biomedical Sciences, Tufts University School of Medicine, Boston, MA, USA. ryan.tewhey@jax.org.

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Classifications MeSH