New Candidates for Autism/Intellectual Disability Identified by Whole-Exome Sequencing.


Journal

International journal of molecular sciences
ISSN: 1422-0067
Titre abrégé: Int J Mol Sci
Pays: Switzerland
ID NLM: 101092791

Informations de publication

Date de publication:
14 Dec 2021
Historique:
received: 29 11 2021
revised: 07 12 2021
accepted: 10 12 2021
entrez: 24 12 2021
pubmed: 25 12 2021
medline: 11 1 2022
Statut: epublish

Résumé

Intellectual disability (ID) is characterized by impairments in the cognitive processes and in the tasks of daily life. It encompasses a clinically and genetically heterogeneous group of neurodevelopmental disorders often associated with autism spectrum disorder (ASD). Social and communication abilities are strongly compromised in ASD. The prevalence of ID/ASD is 1-3%, and approximately 30% of the patients remain without a molecular diagnosis. Considering the extreme genetic locus heterogeneity, next-generation sequencing approaches have provided powerful tools for candidate gene identification. Molecular diagnosis is crucial to improve outcome, prevent complications, and hopefully start a therapeutic approach. Here, we performed parent-offspring trio whole-exome sequencing (WES) in a cohort of 60 mostly syndromic ID/ASD patients and we detected 8 pathogenic variants in genes already known to be associated with ID/ASD (

Identifiants

pubmed: 34948243
pii: ijms222413439
doi: 10.3390/ijms222413439
pmc: PMC8707363
pii:
doi:

Types de publication

Clinical Trial Journal Article

Langues

eng

Sous-ensembles de citation

IM

Références

Genet Med. 2020 Jan;22(1):170-180
pubmed: 31332282
Brain Sci. 2021 Jul 16;11(7):
pubmed: 34356170
J Intellect Disabil Res. 2004 Mar;48(Pt 3):262-7
pubmed: 15025669
Clin Genet. 2020 Nov;98(5):433-444
pubmed: 32335911
Pediatrics. 2014 Sep;134(3):e903-18
pubmed: 25157020
Nat Rev Neurosci. 2015 Sep;16(9):551-63
pubmed: 26289574
Transl Pediatr. 2020 Feb;9(Suppl 1):S55-S65
pubmed: 32206584
Front Hum Neurosci. 2013 Oct 30;7:733
pubmed: 24198778
Nature. 2012 Apr 04;485(7397):237-41
pubmed: 22495306
Front Cell Neurosci. 2019 Aug 20;13:385
pubmed: 31481879
Neurosci Biobehav Rev. 2014 Oct;46 Pt 2:161-74
pubmed: 24709068
J Neurosci Res. 1988 Sep;21(1):62-70
pubmed: 2464072
Eur J Neurosci. 2008 Oct;28(7):1362-76
pubmed: 18973563
Cell Rep. 2015 Jan 13;10(2):148-61
pubmed: 25558065
Am J Med Genet A. 2017 Aug;173(8):2226-2230
pubmed: 28602030
J Biol Chem. 1997 Dec 12;272(50):31625-9
pubmed: 9395502
Mol Autism. 2019 Aug 7;10:33
pubmed: 31406558
Mol Cell Neurosci. 2008 May;38(1):66-79
pubmed: 18353676
Behav Anal Pract. 2010 Fall;3(2):4-12
pubmed: 22532888
J Autism Dev Disord. 2015 Apr;45(4):966-74
pubmed: 25239176
J Intellect Disabil Res. 2001 Dec;45(Pt 6):467-83
pubmed: 11737534
Bioinformatics. 2010 Mar 1;26(5):589-95
pubmed: 20080505
Nat Genet. 2021 Aug;53(8):1125-1134
pubmed: 34312540
Front Pediatr. 2021 Feb 19;9:526779
pubmed: 33681094
Psychiatr Danub. 2009 Mar;21(1):68-71
pubmed: 19270624
Case Rep Ophthalmol Med. 2012;2012:380863
pubmed: 23091761
Lancet. 2014 Mar 8;383(9920):896-910
pubmed: 24074734
Am J Hum Genet. 2016 Mar 3;98(3):541-552
pubmed: 26942287
J Cell Biol. 1995 Sep;130(5):1171-9
pubmed: 7657701
Cell. 1983 Oct;34(3):799-806
pubmed: 6194889
Genet Med. 2016 Sep;18(9):898-905
pubmed: 26795593
J Neurochem. 1988 Dec;51(6):1737-45
pubmed: 2460587
Nature. 2010 Jun 10;465(7299):728-35
pubmed: 20535202
DNA Res. 2002 Apr 30;9(2):47-57
pubmed: 12056414
Hum Genet. 2007 Nov;122(3-4):373-81
pubmed: 17653769
BMC Bioinformatics. 2010 Nov 08;11:548
pubmed: 21059217
Lancet. 2018 Aug 11;392(10146):508-520
pubmed: 30078460
Neurosci Bull. 2017 Apr;33(2):183-193
pubmed: 28213805
Cold Spring Harb Perspect Med. 2017 Mar 1;7(3):
pubmed: 28250017
Prim Care Companion J Clin Psychiatry. 2010;12(2):
pubmed: 20694130
Am J Hum Genet. 2001 Jul;69(1):25-34
pubmed: 11398101
Dialogues Clin Neurosci. 2012 Sep;14(3):281-92
pubmed: 23226953
Hum Genet. 2008 Oct;124(3):215-23
pubmed: 18719945
Ont Health Technol Assess Ser. 2020 Mar 6;20(11):1-178
pubmed: 32194879
Proc Natl Acad Sci U S A. 2006 Dec 26;103(52):19719-24
pubmed: 17172445
Dis Model Mech. 2019 May 13;12(5):
pubmed: 31088981
Acta Biomed. 2020 Nov 09;91(13-S):e2020003
pubmed: 33170170

Auteurs

Lucia Pia Bruno (LP)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.

Gabriella Doddato (G)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.

Floriana Valentino (F)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.

Margherita Baldassarri (M)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.

Rossella Tita (R)

Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Chiara Fallerini (C)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.

Mirella Bruttini (M)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Caterina Lo Rizzo (C)

Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Maria Antonietta Mencarelli (MA)

Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Francesca Mari (F)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Anna Maria Pinto (AM)

Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Francesca Fava (F)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Alessandra Fabbiani (A)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Vittoria Lamacchia (V)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Anna Carrer (A)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Valentina Caputo (V)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Stefania Granata (S)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Elisa Benetti (E)

Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.

Kristina Zguro (K)

Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.

Simone Furini (S)

Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.

Alessandra Renieri (A)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

Francesca Ariani (F)

Medical Genetics, University of Siena, 53100 Siena, Italy.
Med Biotech Hub and Competence Center, Department of Medical Biotechnologies, University of Siena, 53100 Siena, Italy.
Genetica Medica, Azienda Ospedaliera Universitaria Senese, 53100 Siena, Italy.

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