Accurate de novo design of membrane-traversing macrocycles.

computational design membrane permeability oral bioavailability peptide design

Journal

Cell
ISSN: 1097-4172
Titre abrégé: Cell
Pays: United States
ID NLM: 0413066

Informations de publication

Date de publication:
15 09 2022
Historique:
received: 29 12 2021
revised: 01 05 2022
accepted: 21 07 2022
pubmed: 31 8 2022
medline: 21 9 2022
entrez: 30 8 2022
Statut: ppublish

Résumé

We use computational design coupled with experimental characterization to systematically investigate the design principles for macrocycle membrane permeability and oral bioavailability. We designed 184 6-12 residue macrocycles with a wide range of predicted structures containing noncanonical backbone modifications and experimentally determined structures of 35; 29 are very close to the computational models. With such control, we show that membrane permeability can be systematically achieved by ensuring all amide (NH) groups are engaged in internal hydrogen bonding interactions. 84 designs over the 6-12 residue size range cross membranes with an apparent permeability greater than 1 × 10

Identifiants

pubmed: 36041435
pii: S0092-8674(22)00922-9
doi: 10.1016/j.cell.2022.07.019
pmc: PMC9490236
pii:
doi:

Substances chimiques

Amides 0
Lipids 0
Peptides 0
Hydrogen 7YNJ3PO35Z

Types de publication

Journal Article Research Support, Non-U.S. Gov't Research Support, N.I.H., Extramural Research Support, U.S. Gov't, Non-P.H.S.

Langues

eng

Sous-ensembles de citation

IM

Pagination

3520-3532.e26

Subventions

Organisme : NIGMS NIH HHS
ID : P30 GM124165
Pays : United States
Organisme : NIGMS NIH HHS
ID : R01 GM120574
Pays : United States
Organisme : NIGMS NIH HHS
ID : T32 GM007750
Pays : United States
Organisme : NIGMS NIH HHS
ID : F32 GM120791
Pays : United States
Organisme : Howard Hughes Medical Institute
Pays : United States
Organisme : NIA NIH HHS
ID : R01 AG063845
Pays : United States
Organisme : NIGMS NIH HHS
ID : R35 GM141818
Pays : United States

Commentaires et corrections

Type : CommentIn

Informations de copyright

Copyright © 2022 The Author(s). Published by Elsevier Inc. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of interests V.K.M. is a cofounder and shareholder of Menten AI, a biotechnology company. G.T.M. is a cofounder of Nexomics Biosciences, Inc., a structural biology contract research organization. A provisional patent covering the membrane-permeable peptides described in this paper has been filed by the University of Washington, Seattle. G.B., L.S., and D.B. are cofounders and shareholders of an early-stage biotechnology company that has licensed the provisional patent.

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Auteurs

Gaurav Bhardwaj (G)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA; Department of Medicinal Chemistry, University of Washington, Seattle, WA 98195, USA; Biological Physics, Structure and Design program, University of Washington, Seattle, WA 98195, USA. Electronic address: gauravb@uw.edu.

Jacob O'Connor (J)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA; Biological Physics, Structure and Design program, University of Washington, Seattle, WA 98195, USA; Department of Biochemistry, University of Washington, Seattle, WA 98195, USA.

Stephen Rettie (S)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA; Molecular Cell and Biology program, University of Washington, Seattle, WA 98195, USA.

Yen-Hua Huang (YH)

Institute for Molecular Bioscience, Australian Research Council Centre of Excellence for Innovations in Peptide and Protein Science, The University of Queensland, Brisbane, QLD 4072, Australia.

Theresa A Ramelot (TA)

Department of Chemistry and Chemical Biology and Center for Biotechnology and Interdisciplinary Sciences, Rensselaer Polytechnic Institute, Troy, NY 12180, USA.

Vikram Khipple Mulligan (VK)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Gizem Gokce Alpkilic (GG)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA; Department of Medicinal Chemistry, University of Washington, Seattle, WA 98195, USA; Molecular Engineering and Sciences Program, University of Washington, Seattle, WA 98195, USA.

Jonathan Palmer (J)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA; Department of Medicinal Chemistry, University of Washington, Seattle, WA 98195, USA.

Asim K Bera (AK)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Matthew J Bick (MJ)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Maddalena Di Piazza (M)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA; Department of Medicinal Chemistry, University of Washington, Seattle, WA 98195, USA.

Xinting Li (X)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Parisa Hosseinzadeh (P)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Timothy W Craven (TW)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA; Department of Biochemistry, University of Washington, Seattle, WA 98195, USA.

Roberto Tejero (R)

Departamento de Quίmica Fίsica, Universidad de Valencia, Avenida Dr. Moliner 50, Burjassot, 46100 Valencia, Spain.

Anna Lauko (A)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA; Biological Physics, Structure and Design program, University of Washington, Seattle, WA 98195, USA; Department of Biochemistry, University of Washington, Seattle, WA 98195, USA.

Ryan Choi (R)

Department of Medicine, Division of Allergy and Infectious Disease, University of Washington, Seattle, WA, USA.

Calina Glynn (C)

Department of Chemistry and Biochemistry, University of California-Los Angeles, Los Angeles, CA, USA.

Linlin Dong (L)

Takeda Pharmaceuticals Inc., Cambridge, MA, USA.

Robert Griffin (R)

Takeda Pharmaceuticals Inc., Cambridge, MA, USA.

Wesley C van Voorhis (WC)

Department of Medicine, Division of Allergy and Infectious Disease, University of Washington, Seattle, WA, USA.

Jose Rodriguez (J)

Department of Chemistry and Biochemistry, University of California-Los Angeles, Los Angeles, CA, USA.

Lance Stewart (L)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Gaetano T Montelione (GT)

Department of Chemistry and Chemical Biology and Center for Biotechnology and Interdisciplinary Sciences, Rensselaer Polytechnic Institute, Troy, NY 12180, USA.

David Craik (D)

Institute for Molecular Bioscience, Australian Research Council Centre of Excellence for Innovations in Peptide and Protein Science, The University of Queensland, Brisbane, QLD 4072, Australia.

David Baker (D)

Institute for Protein Design, University of Washington, Seattle, WA 98195, USA; Department of Biochemistry, University of Washington, Seattle, WA 98195, USA; Howard Hughes Medical Institute, University of Washington, Seattle, WA 98195, USA. Electronic address: dabaker@uw.edu.

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Classifications MeSH