A Randomized Phase II Trial of Epigenetic Priming with Guadecitabine and Carboplatin in Platinum-resistant, Recurrent Ovarian Cancer.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
01 03 2020
Historique:
received: 30 05 2019
revised: 16 09 2019
accepted: 05 12 2019
pubmed: 14 12 2019
medline: 5 1 2021
entrez: 14 12 2019
Statut: ppublish

Résumé

Platinum resistance in ovarian cancer is associated with epigenetic modifications. Hypomethylating agents (HMA) have been studied as carboplatin resensitizing agents in ovarian cancer. This randomized phase II trial compared guadecitabine, a second-generation HMA, and carboplatin (G+C) against second-line chemotherapy in women with measurable or detectable platinum-resistant ovarian cancer. Patients received either G+C (guadecitabine 30 mg/m Of 100 patients treated, 51 received G+C and 49 received TC, of which 27 crossed over to G+C. The study did not meet its primary endpoint as the median PFS was not statistically different between arms (16.3 weeks vs. 9.1 weeks in the G+C and TC groups, respectively; Although this trial did not show superiority for PFS of G+C versus TC, the 6-month PFS increased in G+C treated patients. Further refinement of this strategy should focus on identification of predictive markers for patient selection.

Identifiants

pubmed: 31831561
pii: 1078-0432.CCR-19-1638
doi: 10.1158/1078-0432.CCR-19-1638
pmc: PMC7056559
mid: NIHMS1546537
doi:

Substances chimiques

liposomal doxorubicin 0
Deoxycytidine 0W860991D6
guadecitabine 2KT4YN1DP7
Polyethylene Glycols 3WJQ0SDW1A
Topotecan 7M7YKX2N15
Doxorubicin 80168379AG
Carboplatin BG3F62OND5
Azacitidine M801H13NRU
Paclitaxel P88XT4IS4D
Gemcitabine 0

Banques de données

ClinicalTrials.gov
['NCT01696032']

Types de publication

Clinical Trial, Phase II Journal Article Multicenter Study Randomized Controlled Trial Research Support, N.I.H., Extramural Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1009-1016

Subventions

Organisme : NCI NIH HHS
ID : R01 CA182832
Pays : United States

Informations de copyright

©2019 American Association for Cancer Research.

Références

Cancer Lett. 2006 Sep 28;241(2):213-20
pubmed: 16303245
Eur J Cancer. 2009 Jan;45(2):228-47
pubmed: 19097774
J Clin Oncol. 2014 May 1;32(13):1302-8
pubmed: 24637997
J Clin Oncol. 2005 Jun 10;23(17):3948-56
pubmed: 15883410
BMC Med Genomics. 2008 Sep 30;1:47
pubmed: 18826610
Adv Exp Med Biol. 2008;622:35-51
pubmed: 18546617
N Engl J Med. 2005 Mar 24;352(12):1268-9; author reply 1268-9
pubmed: 15791705
Epigenetics. 2015;10(8):736-48
pubmed: 26098711
J Clin Oncol. 2007 Oct 10;25(29):4603-9
pubmed: 17925555
Gynecol Oncol. 2004 Dec;95(3):686-90
pubmed: 15581982
Cancer Immunol Res. 2014 Jan;2(1):37-49
pubmed: 24535937
Lancet Oncol. 2015 Sep;16(9):1099-1110
pubmed: 26296954
Oncotarget. 2017 Jan 10;8(2):2949-2959
pubmed: 27936464
Cancer. 2010 Sep 1;116(17):4043-53
pubmed: 20564122
Clin Cancer Res. 2018 Dec 15;24(24):6160-6167
pubmed: 30097434
Clin Cancer Res. 2014 Dec 15;20(24):6504-16
pubmed: 25316809
Cancer. 2011 Apr 15;117(8):1661-9
pubmed: 21472713
Gynecol Oncol. 2008 Apr;109(1):129-39
pubmed: 18234305
Cancer Res. 2000 Nov 1;60(21):6039-44
pubmed: 11085525
Cancer Res. 2004 Sep 15;64(18):6476-81
pubmed: 15374957
Clin Cancer Res. 2018 May 15;24(10):2285-2293
pubmed: 29500276
J Clin Oncol. 2011 Jan 10;29(2):242-8
pubmed: 21115872
Endocrinology. 2009 Sep;150(9):4003-11
pubmed: 19574400
Clin Cancer Res. 2004 Jun 1;10(11):3919-26
pubmed: 15173101
JCI Insight. 2018 Dec 6;3(23):
pubmed: 30518684
Br J Cancer. 2014 Apr 15;110(8):1923-9
pubmed: 24642620
Mol Cancer Ther. 2003 Aug;2(8):721-8
pubmed: 12939461
Cancer Res. 2018 Feb 1;78(3):631-644
pubmed: 29229600
Cancer Res. 2014 Sep 1;74(17):4922-36
pubmed: 25035395
J Clin Oncol. 2003 May 15;21(10 Suppl):187s-193s
pubmed: 12743133
Oncotarget. 2014 Jun 15;5(11):3579-89
pubmed: 25003579
Cell Cycle. 2009 Jan 1;8(1):158-66
pubmed: 19158483
Cancer Res. 2012 May 1;72(9):2197-205
pubmed: 22549947
Br J Cancer. 2002 Oct 7;87(8):815-24
pubmed: 12373593

Auteurs

Amit M Oza (AM)

Princess Margaret Cancer Centre, University Health Network, University of Toronto, Toronto Canada.

Ursula A Matulonis (UA)

Dana-Farber Cancer Institute, Boston, Massachusetts.

Angeles Alvarez Secord (A)

Duke Cancer Institute, Durham, North Carolina.

John Nemunaitis (J)

University of Toledo College of Medicine and Life Sciences, Toledo, Ohio.

Lynda D Roman (LD)

USC Norris Comprehensive Cancer Center, Los Angeles, California.

Sarah P Blagden (SP)

University of Oxford, Oxford, United Kingdom.

Susana Banerjee (S)

Royal Marsden NHS Foundation Trust, London, United Kingdom.

William P McGuire (WP)

Virginia Commonwealth University, Richmond, Virginia.

Sharad Ghamande (S)

Augusta University (Georgia Regents University), Augusta, Georgia.

Michael J Birrer (MJ)

University of Alabama at Birmingham, Birmingham, Alabama.

Gini F Fleming (GF)

The University of Chicago Medicine, Chicago, Illinois.

Merry Jennifer Markham (MJ)

University of Florida, Gainesville, Florida.

Hal W Hirte (HW)

Juravinski Cancer Centre, Hamilton, Canada.

Diane M Provencher (DM)

Centre Hospitalier de l'Université de Montréal, Université de Montréal, Montréal, Canada.

Bristi Basu (B)

Department of Oncology, University of Cambridge and Cambridge University Hospitals NHS Foundation Trust, Cambridge, United Kingdom.

Rebecca Kristeleit (R)

Cancer Institute University College London, UCL, United Kingdom.

Deborah K Armstrong (DK)

Johns Hopkins Kimmel Cancer Center, Baltimore, Maryland.

Benjamin Schwartz (B)

Northwell Health Gynecologic Oncology, Bay Shore, New York.

Patricia Braly (P)

Women's Cancer Care, Covington, Los Angeles.

Geoff D Hall (GD)

St James University Hospital, Leeds, United Kingdom.

Kenneth P Nephew (KP)

Indiana University School of Medicine, IU Simon Cancer Center, Bloomington, Indiana.

Simone Jueliger (S)

Astex Pharmaceuticals, Cambridge, United Kingdom.

Aram Oganesian (A)

Astex Pharmaceuticals Inc., Pleasanton, California.

Sue Naim (S)

Astex Pharmaceuticals Inc., Pleasanton, California.

Yong Hao (Y)

Astex Pharmaceuticals Inc., Pleasanton, California.

Harold Keer (H)

Astex Pharmaceuticals Inc., Pleasanton, California.

Mohammad Azab (M)

Astex Pharmaceuticals Inc., Pleasanton, California.

Daniela Matei (D)

Northwestern University Feinberg School of Medicine, Chicago, Illinois. Daniela.matei@northwestern.edu.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH