Identification of a Small-Molecule Inhibitor That Disrupts the SIX1/EYA2 Complex, EMT, and Metastasis.


Journal

Cancer research
ISSN: 1538-7445
Titre abrégé: Cancer Res
Pays: United States
ID NLM: 2984705R

Informations de publication

Date de publication:
15 06 2020
Historique:
received: 07 02 2020
revised: 19 03 2020
accepted: 22 04 2020
pubmed: 29 4 2020
medline: 11 11 2020
entrez: 29 4 2020
Statut: ppublish

Résumé

Metastasis is the major cause of mortality for patients with cancer, and dysregulation of developmental signaling pathways can significantly contribute to the metastatic process. The Sine oculis homeobox homolog 1 (SIX1)/eyes absent (EYA) transcriptional complex plays a critical role in the development of multiple organs and is typically downregulated after development is complete. In breast cancer, aberrant expression of SIX1 has been demonstrated to stimulate metastasis through activation of TGFβ signaling and subsequent induction of epithelial-mesenchymal transition (EMT). In addition, SIX1 can induce metastasis via non-cell autonomous means, including activation of GLI-signaling in neighboring tumor cells and activation of VEGFC-induced lymphangiogenesis. Thus, targeting SIX1 would be expected to inhibit metastasis while conferring limited side effects. However, transcription factors are notoriously difficult to target, and thus novel approaches to inhibit their action must be taken. Here we identified a novel small molecule compound, NCGC00378430 (abbreviated as 8430), that reduces the SIX1/EYA2 interaction. 8430 partially reversed transcriptional and metabolic profiles mediated by SIX1 overexpression and reversed SIX1-induced TGFβ signaling and EMT. 8430 was well tolerated when delivered to mice and significantly suppressed breast cancer-associated metastasis

Identifiants

pubmed: 32341035
pii: 0008-5472.CAN-20-0435
doi: 10.1158/0008-5472.CAN-20-0435
pmc: PMC7510951
mid: NIHMS1589489
doi:

Substances chimiques

Antineoplastic Agents 0
BRCA1 Protein 0
BRCA1 protein, human 0
Homeodomain Proteins 0
Intracellular Signaling Peptides and Proteins 0
Nuclear Proteins 0
SIX1 protein, human 0
EYA2 protein, human EC 3.1.3.48
Protein Tyrosine Phosphatases EC 3.1.3.48

Types de publication

Journal Article Research Support, N.I.H., Extramural Research Support, N.I.H., Intramural Research Support, Non-U.S. Gov't Research Support, U.S. Gov't, Non-P.H.S.

Langues

eng

Sous-ensembles de citation

IM

Pagination

2689-2702

Subventions

Organisme : NINDS NIH HHS
ID : R01 NS108396
Pays : United States
Organisme : NIH HHS
ID : K01 OD022982
Pays : United States
Organisme : NIDA NIH HHS
ID : R03 DA033174
Pays : United States
Organisme : NCI NIH HHS
ID : R01 CA224867
Pays : United States
Organisme : NCI NIH HHS
ID : P30 CA046934
Pays : United States
Organisme : NCI NIH HHS
ID : F99 CA234940
Pays : United States
Organisme : NCI NIH HHS
ID : K00 CA234940
Pays : United States
Organisme : NIGMS NIH HHS
ID : T32 GM007635
Pays : United States
Organisme : NCI NIH HHS
ID : R21 CA185752
Pays : United States
Organisme : NIH HHS
ID : S10 OD027023
Pays : United States

Informations de copyright

©2020 American Association for Cancer Research.

Références

Int J Cancer. 2010 Aug 15;127(4):859-72
pubmed: 20013809
Oncogene. 2012 Feb 2;31(5):552-62
pubmed: 21706047
Cancer Res. 2014 Oct 1;74(19):5597-607
pubmed: 25142796
Trends Immunol. 2019 Jun;40(6):511-523
pubmed: 31053497
OMICS. 2012 May;16(5):284-7
pubmed: 22455463
J Clin Invest. 2009 Sep;119(9):2663-77
pubmed: 19726883
J Clin Med. 2016 Jan 27;5(2):
pubmed: 26828526
Oncogene. 2010 Jun 24;29(25):3715-22
pubmed: 20418914
Biotechniques. 2014 May;56(5):217-28
pubmed: 24919231
Br J Cancer. 2006 Oct 23;95(8):1050-5
pubmed: 17008870
Development. 2003 Jul;130(14):3085-94
pubmed: 12783782
Biosci Rep. 2019 Apr 30;39(4):
pubmed: 30962263
Cancer Cell. 2018 Mar 12;33(3):368-385.e7
pubmed: 29455928
Genome Biol. 2014;15(12):550
pubmed: 25516281
Bioinformatics. 2011 Jun 15;27(12):1739-40
pubmed: 21546393
J Clin Invest. 2012 May;122(5):1895-906
pubmed: 22466647
Expert Opin Ther Targets. 2015 Feb;19(2):213-25
pubmed: 25555392
Cancer Res. 2005 Apr 1;65(7):2668-75
pubmed: 15805264
Nat Commun. 2018 Mar 13;9(1):1047
pubmed: 29535359
Cancer Cell. 2015 Feb 9;27(2):298-311
pubmed: 25670083
Adv Cancer Res. 2019;141:1-42
pubmed: 30691681
Nat Rev Mol Cell Biol. 2019 Feb;20(2):69-84
pubmed: 30459476
Hum Mol Genet. 1999 Jan;8(1):11-23
pubmed: 9887327
Assay Drug Dev Technol. 2009 Feb;7(1):90-2
pubmed: 19382891
Nat Genet. 1997 Feb;15(2):157-64
pubmed: 9020840
Biomol Detect Quantif. 2015 May 20;4:10-6
pubmed: 27077033
Biochem Biophys Res Commun. 2014 Apr 4;446(2):549-54
pubmed: 24613848
Cancer Res. 2007 Apr 1;67(7):3036-42
pubmed: 17409410
Nat Med. 2004 Feb;10(2):175-81
pubmed: 14704789
J Biomol Screen. 2015 Jun;20(5):663-72
pubmed: 25477201
Amino Acids. 2015 Nov;47(11):2345-57
pubmed: 26058356
Nat Struct Mol Biol. 2013 Apr;20(4):447-53
pubmed: 23435380
Cancer Res. 2005 Feb 1;65(3):925-32
pubmed: 15705892
Nat Rev Cancer. 2009 Jan;9(1):28-39
pubmed: 19104514
Nat Rev Cancer. 2019 Nov;19(11):611-624
pubmed: 31511663
Cell Death Dis. 2017 Apr 6;8(4):e2728
pubmed: 28383549
Cancer Res. 2008 Apr 1;68(7):2204-13
pubmed: 18381426
Cell. 2017 Feb 9;168(4):629-643
pubmed: 28187285
Carcinogenesis. 2014 Jun;35(6):1379-88
pubmed: 24574515
Nat Commun. 2017 Jun 12;8:15773
pubmed: 28604738
Biochem Biophys Res Commun. 2019 Jul 12;515(1):85-91
pubmed: 31128917
J Clin Invest. 2009 Sep;119(9):2678-90
pubmed: 19726885
Cancer Res. 2010 Dec 15;70(24):10371-80
pubmed: 21056993
Proc Natl Acad Sci U S A. 1998 Nov 24;95(24):14220-5
pubmed: 9826681
Oncogene. 2012 Nov 22;31(47):4923-34
pubmed: 22286765
Carcinogenesis. 2017 Mar 1;38(3):281-292
pubmed: 28199476
Proc Natl Acad Sci U S A. 1998 Oct 13;95(21):12608-13
pubmed: 9770533
Arch Biochem Biophys. 2015 Oct 1;583:18-26
pubmed: 26247838
Breast Cancer Res. 2012 Jul 05;14(4):R100
pubmed: 22765220
J Mammary Gland Biol Neoplasia. 2010 Jun;15(2):117-34
pubmed: 20490631
J Cell Mol Med. 2019 Jul;23(7):4523-4533
pubmed: 31044528
Genome Res. 1997 Feb;7(2):128-41
pubmed: 9049631
J Clin Invest. 2015 May;125(5):1780-9
pubmed: 25932675
Cancer Cell. 2015 Feb 9;27(2):286-97
pubmed: 25670082

Auteurs

Hengbo Zhou (H)

Department of Pharmacology, University of Colorado Anschutz Medical Campus, Aurora, Colorado.
Cancer Biology Program, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Melanie A Blevins (MA)

Department of Biochemistry and Molecular Genetics, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Jessica Y Hsu (JY)

Department of Pharmacology, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Deguang Kong (D)

Department of Pharmacology, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Matthew D Galbraith (MD)

Department of Pharmacology, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Andrew Goodspeed (A)

Department of Pharmacology, University of Colorado Anschutz Medical Campus, Aurora, Colorado.
University of Colorado Cancer Center, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Rachel Culp-Hill (R)

Department of Biochemistry and Molecular Genetics, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Michael U J Oliphant (MUJ)

Department of Pharmacology, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Dominique Ramirez (D)

Flint Animal Cancer Center, Colorado State University, Fort Collins, Colorado.

Lingdi Zhang (L)

Department of Biochemistry and Molecular Genetics, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Jennyvette Trinidad-Pineiro (J)

Department of Biochemistry and Molecular Genetics, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Lesley Mathews Griner (L)

Early Translation Branch, National Center for Advancing Translational Sciences, National Institutes of Health, Rockville, Maryland.

Rebecca King (R)

Early Translation Branch, National Center for Advancing Translational Sciences, National Institutes of Health, Rockville, Maryland.

Elena Barnaeva (E)

Early Translation Branch, National Center for Advancing Translational Sciences, National Institutes of Health, Rockville, Maryland.

Xin Hu (X)

Early Translation Branch, National Center for Advancing Translational Sciences, National Institutes of Health, Rockville, Maryland.

Noel T Southall (NT)

Early Translation Branch, National Center for Advancing Translational Sciences, National Institutes of Health, Rockville, Maryland.

Marc Ferrer (M)

Early Translation Branch, National Center for Advancing Translational Sciences, National Institutes of Health, Rockville, Maryland.

Daniel L Gustafson (DL)

University of Colorado Cancer Center, University of Colorado Anschutz Medical Campus, Aurora, Colorado.
Flint Animal Cancer Center, Colorado State University, Fort Collins, Colorado.

Daniel P Regan (DP)

University of Colorado Cancer Center, University of Colorado Anschutz Medical Campus, Aurora, Colorado.
Flint Animal Cancer Center, Colorado State University, Fort Collins, Colorado.

Angelo D'Alessandro (A)

Department of Biochemistry and Molecular Genetics, University of Colorado Anschutz Medical Campus, Aurora, Colorado.
University of Colorado Cancer Center, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

James C Costello (JC)

Department of Pharmacology, University of Colorado Anschutz Medical Campus, Aurora, Colorado.
University of Colorado Cancer Center, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Samarjit Patnaik (S)

Early Translation Branch, National Center for Advancing Translational Sciences, National Institutes of Health, Rockville, Maryland.

Juan Marugan (J)

Early Translation Branch, National Center for Advancing Translational Sciences, National Institutes of Health, Rockville, Maryland.

Rui Zhao (R)

Department of Biochemistry and Molecular Genetics, University of Colorado Anschutz Medical Campus, Aurora, Colorado. heide.ford@cuanschutz.edu Rui.Zhao@cuanschutz.edu.
University of Colorado Cancer Center, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

Heide L Ford (HL)

Department of Pharmacology, University of Colorado Anschutz Medical Campus, Aurora, Colorado. heide.ford@cuanschutz.edu Rui.Zhao@cuanschutz.edu.
University of Colorado Cancer Center, University of Colorado Anschutz Medical Campus, Aurora, Colorado.

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