Journal

Journal of medical genetics
ISSN: 1468-6244
Titre abrégé: J Med Genet
Pays: England
ID NLM: 2985087R

Informations de publication

Date de publication:
05 2021
Historique:
received: 09 01 2020
revised: 02 04 2020
accepted: 22 04 2020
pubmed: 11 6 2020
medline: 19 1 2022
entrez: 11 6 2020
Statut: ppublish

Résumé

The nucleotide binding protein-like ( Whole exome sequencing was used to identify patients with compound heterozygous The previously reported c.815-27T>C branch-site mutation was found in all four families. In prior patients, c.166G>A [p.G56R] was always found We report on five new patients with

Sections du résumé

BACKGROUND
The nucleotide binding protein-like (
METHODS
Whole exome sequencing was used to identify patients with compound heterozygous
RESULTS
The previously reported c.815-27T>C branch-site mutation was found in all four families. In prior patients, c.166G>A [p.G56R] was always found
CONCLUSION
We report on five new patients with

Identifiants

pubmed: 32518176
pii: jmedgenet-2020-106846
doi: 10.1136/jmedgenet-2020-106846
doi:

Substances chimiques

Mitochondrial Proteins 0
NUBPL protein, human 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't Review

Langues

eng

Sous-ensembles de citation

IM

Pagination

314-325

Subventions

Organisme : Biotechnology and Biological Sciences Research Council
ID : BBS/E/J/000PR9790
Pays : United Kingdom

Informations de copyright

© Author(s) (or their employer(s)) 2021. No commercial re-use. See rights and permissions. Published by BMJ.

Déclaration de conflit d'intérêts

Competing interests: EH and PSE are employees of Population Bio. BRC, SW, RK, ST and EC are employees of Ambry Genetics.

Auteurs

Virginia Kimonis (V)

Division of Genetics and Metabolism, Department of Pediatrics, University of California Irvine, Irvine, California, USA vkimonis@uci.edu pegeis@populationbio.com.

Rehab Al Dubaisi (R)

Division of Genetics and Metabolism, Department of Pediatrics, University of California Irvine, Irvine, California, USA.

Andrew E Maclean (AE)

Department of Biological Chemistry, John Innes Centre, Norwich, Norfolk, UK.
Wellcome Centre for Integrative Parasitology, University of Glasgow, Glasgow, Glasgow, UK.

Kathy Hall (K)

Division of Genetics and Metabolism, Department of Pediatrics, University of California Irvine, Irvine, California, USA.

Lan Weiss (L)

Division of Genetics and Metabolism, Department of Pediatrics, University of California Irvine, Irvine, California, USA.

Alexander E Stover (AE)

CHOC National Human Neural Stem Cell Resource, Children's Hospital of Orange County Research Institute, Orange, California, USA.

Philip H Schwartz (PH)

CHOC National Human Neural Stem Cell Resource, Children's Hospital of Orange County Research Institute, Orange, California, USA.

Bethany Berg (B)

Division of Genetics and Metabolism, Department of Pediatrics, University of California Irvine, Irvine, California, USA.

Cheng Cheng (C)

Division of Genetics and Metabolism, Department of Pediatrics, University of California Irvine, Irvine, California, USA.

Sumit Parikh (S)

Center for Pediatric Neurology, Cleveland Clinic, Cleveland, Ohio, USA.

Blair R Conner (BR)

Ambry Genetics Corp, Aliso Viejo, California, USA.

Sitao Wu (S)

Ambry Genetics Corp, Aliso Viejo, California, USA.

Anton N Hasso (AN)

Radiological Sciences, University of California Irvine School of Medicine, Irvine, California, USA.

Daryl A Scott (DA)

Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas, USA.
Department of Molecular Physiology and Biophysics, Baylor College of Medicine, Houston, Texas, USA.

Mary Kay Koenig (MK)

Department of Pediatrics, University of Texas McGovern Medical School, Houston, Texas, USA.

Rachid Karam (R)

Ambry Genetics Corp, Aliso Viejo, California, USA.

Sha Tang (S)

Ambry Genetics Corp, Aliso Viejo, California, USA.

Moyra Smith (M)

Division of Genetics and Metabolism, Department of Pediatrics, University of California Irvine, Irvine, California, USA.

Elizabeth Chao (E)

Division of Genetics and Metabolism, Department of Pediatrics, University of California Irvine, Irvine, California, USA.
Ambry Genetics Corp, Aliso Viejo, California, USA.

Janneke Balk (J)

Department of Biological Chemistry, John Innes Centre, Norwich, Norfolk, UK.

Eli Hatchwell (E)

Population Bio UK, Inc, Begbroke, Oxfordshire, UK.

Peggy S Eis (PS)

Population Bio, Inc, New York, New York, USA vkimonis@uci.edu pegeis@populationbio.com.

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Classifications MeSH