Ultrarare heterozygous pathogenic variants of genes causing dominant forms of early-onset deafness underlie severe presbycusis.


Journal

Proceedings of the National Academy of Sciences of the United States of America
ISSN: 1091-6490
Titre abrégé: Proc Natl Acad Sci U S A
Pays: United States
ID NLM: 7505876

Informations de publication

Date de publication:
08 12 2020
Historique:
pubmed: 25 11 2020
medline: 22 1 2021
entrez: 24 11 2020
Statut: ppublish

Résumé

Presbycusis, or age-related hearing loss (ARHL), is a major public health issue. About half the phenotypic variance has been attributed to genetic factors. Here, we assessed the contribution to presbycusis of ultrarare pathogenic variants, considered indicative of Mendelian forms. We focused on severe presbycusis without environmental or comorbidity risk factors and studied multiplex family age-related hearing loss (mARHL) and simplex/sporadic age-related hearing loss (sARHL) cases and controls with normal hearing by whole-exome sequencing. Ultrarare variants (allele frequency [AF] < 0.0001) of 35 genes responsible for autosomal dominant early-onset forms of deafness, predicted to be pathogenic, were detected in 25.7% of mARHL and 22.7% of sARHL cases vs. 7.5% of controls (

Identifiants

pubmed: 33229591
pii: 2010782117
doi: 10.1073/pnas.2010782117
pmc: PMC7733833
doi:

Substances chimiques

Membrane Proteins 0
MicroRNAs 0
TMC1 protein, human 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

31278-31289

Déclaration de conflit d'intérêts

The authors declare no competing interest.

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Auteurs

Sophie Boucher (S)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.
Complexité du Vivant, Sorbonne Universités, Université Pierre et Marie Curie, Université Paris 06, 75005 Paris, France.
Centre Hospitalier Universitaire, Service d'Oto-Rhino-Laryngologie et Chirurgie Cervico-Faciale, 49100 Angers, France.
Faculté de Médecine, Unité de Formation et de Recherche Santé, Université d'Angers, 49100 Angers, France.

Fabienne Wong Jun Tai (FWJ)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.

Sedigheh Delmaghani (S)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.

Andrea Lelli (A)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.

Amrit Singh-Estivalet (A)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.
Complexité du Vivant, Sorbonne Universités, Université Pierre et Marie Curie, Université Paris 06, 75005 Paris, France.

Typhaine Dupont (T)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.

Magali Niasme-Grare (M)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.
Service de Biochimie et Biologie Moléculaire, Hôpital d'Enfants Armand-Trousseau, Assistance Publique-Hôpitaux de Paris (AP-HP), 75012 Paris, France.

Vincent Michel (V)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.

Nicolas Wolff (N)

Unité Récepteurs-Canaux, Institut Pasteur, 75015 Paris, France.

Amel Bahloul (A)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.

Yosra Bouyacoub (Y)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.

Didier Bouccara (D)

Hôpital Beaujon, Hôpitaux Universitaires Paris Nord val-de-Seine, AP-HP, 92110 Clichy, France.

Bernard Fraysse (B)

Centre Hospitalier Universitaire, Service d'Oto-Rhino-Laryngologie et Chirurgie Cervico-Faciale, Hôpital Larrey, 31400 Toulouse, France.

Olivier Deguine (O)

Centre Hospitalier Universitaire, Service d'Oto-Rhino-Laryngologie et Chirurgie Cervico-Faciale, Hôpital Larrey, 31400 Toulouse, France.

Lionel Collet (L)

Centre Hospitalier Universitaire, Audiologie et Explorations Orofaciales, Hôpital Lyon-Sud, 69495 Lyon, France.

Hung Thai-Van (H)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.
Centre Hospitalier Universitaire, Exploration Fonctionnelle Audiologie et Vestibulaire, Hôpital Edouard Herriot, 69437 Lyon, France.
Claude Bernard University Lyon 1, 69100 Villeurbanne, France.

Eugen Ionescu (E)

Centre Hospitalier Universitaire, Exploration Fonctionnelle Audiologie et Vestibulaire, Hôpital Edouard Herriot, 69437 Lyon, France.

Jean-Louis Kemeny (JL)

Centre Hospitalier Universitaire, Service d'Anatomo-Pathologie, Hôpital Gabriel Montpied, 63000 Clermont-Ferrand, France.

Fabrice Giraudet (F)

Unité Mixte de Recherche (UMR) 1107, INSERM, 63001 Clermont-Ferrand, France.
Laboratoire de Biophysique Neurosensorielle, Faculté de Médecine, Université Clermont Auvergne, 63001 Clermont-Ferrand, France.

Jean-Pierre Lavieille (JP)

Centre Hospitalier Universitaire, Service d'Oto-Rhino-Laryngologie, Hôpital Nord, 13015 Marseille, France.

Arnaud Devèze (A)

Centre Hospitalier Universitaire, Service d'Oto-Rhino-Laryngologie, Hôpital Nord, 13015 Marseille, France.

Anne-Laure Roudevitch-Pujol (AL)

Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts, Centre d'Investigation Clinique, 75012 Paris, France.

Christophe Vincent (C)

Centre Hospitalier Universitaire, Service d'Otologie et Otoneurologie, Hôpital Roger Salengro, 59000 Lille, France.

Christian Renard (C)

Laboratoire d'Audiologie Renard, 59000 Lille, France.

Valérie Franco-Vidal (V)

Centre Hospitalier Universitaire, Service d'Oto-Rhino-Laryngologie et Chirurgie Cervico-Faciale, Hôpital Pellegrin, 33076 Bordeaux, France.

Claire Thibult-Apt (C)

Centre Hospitalier Universitaire, Service d'Oto-Rhino-Laryngologie et Chirurgie Cervico-Faciale, Hôpital Pellegrin, 33076 Bordeaux, France.

Vincent Darrouzet (V)

Centre Hospitalier Universitaire, Service d'Oto-Rhino-Laryngologie et Chirurgie Cervico-Faciale, Hôpital Pellegrin, 33076 Bordeaux, France.

Eric Bizaguet (E)

Laboratoire de Correction Auditive, Eric Bizaguet, 75001 Paris, France.

Arnaud Coez (A)

Laboratoire de Correction Auditive, Eric Bizaguet, 75001 Paris, France.
Commissariat à l'Energie Atomique (CEA)-INSERM U1000 Neuroimaging and Psychiatry, Service Hospitalier Frédéric Joliot, 91400 Orsay, France.
CEA, Direction de Recherche Médicale, Direction des Sciences du Vivant, Service Hospitalier Frédéric-Joliot, 91400 Orsay, France.

Hugues Aschard (H)

Centre de Bioinformatique, Biostatistique et Biologie Intégrative, Institut Pasteur, 75015 Paris, France.

Nicolas Michalski (N)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.

Gaëlle M Lefevre (GM)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.

Anne Aubois (A)

Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts, Centre d'Investigation Clinique, 75012 Paris, France.

Paul Avan (P)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.
Unité Mixte de Recherche (UMR) 1107, INSERM, 63001 Clermont-Ferrand, France.
Laboratoire de Biophysique Neurosensorielle, Faculté de Médecine, Université Clermont Auvergne, 63001 Clermont-Ferrand, France.
Laboratoire de Biophysique, Centre Jean Perrin, 63000 Clermont-Ferrand, France.

Crystel Bonnet (C)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France.
Complexité du Vivant, Sorbonne Universités, Université Pierre et Marie Curie, Université Paris 06, 75005 Paris, France.

Christine Petit (C)

Institut de l'Audition, Institut Pasteur, INSERM, 75012 Paris, France; christine.petit@pasteur.fr.
Collège de France, 75005 Paris, France.

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