Linkage analysis identifies an isolated strabismus locus at 14q12 overlapping with FOXG1 syndrome region.


Journal

Journal of medical genetics
ISSN: 1468-6244
Titre abrégé: J Med Genet
Pays: England
ID NLM: 2985087R

Informations de publication

Date de publication:
01 2022
Historique:
received: 02 06 2020
revised: 05 09 2020
accepted: 29 09 2020
pubmed: 2 12 2020
medline: 9 3 2022
entrez: 1 12 2020
Statut: ppublish

Résumé

Strabismus is a common condition, affecting 1%-4% of individuals. Isolated strabismus has been studied in families with Mendelian inheritance patterns. Despite the identification of multiple loci via linkage analyses, no specific genes have been identified from these studies. The current study is based on a seven-generation family with isolated strabismus inherited in an autosomal dominant manner. A total of 13 individuals from a common ancestor have been included for linkage analysis. Among these, nine are affected and four are unaffected. A single linkage signal has been identified at an 8.5 Mb region of chromosome 14q12 with a multipoint LOD (logarithm of the odds) score of 4.69. Disruption of this locus is known to cause FOXG1 syndrome (or congenital Rett syndrome; OMIM #613454 and *164874), in which 84% of affected individuals present with strabismus. With the incorporation of next-generation sequencing and in-depth bioinformatic analyses, a 4 bp non-coding deletion was prioritised as the top candidate for the observed strabismus phenotype. The deletion is predicted to disrupt regulation of

Identifiants

pubmed: 33257509
pii: jmedgenet-2020-107226
doi: 10.1136/jmedgenet-2020-107226
pmc: PMC8685624
doi:

Substances chimiques

FOXG1 protein, human 0
Forkhead Transcription Factors 0
Nerve Tissue Proteins 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

46-55

Subventions

Organisme : CIHR
ID : GSD-146285
Pays : Canada

Informations de copyright

© Author(s) (or their employer(s)) 2022. Re-use permitted under CC BY-NC. No commercial re-use. See rights and permissions. Published by BMJ.

Déclaration de conflit d'intérêts

Competing interests: None declared.

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Auteurs

Xin Cynthia Ye (XC)

Centre for Molecular Medicine and Therapeutics, The University of British Columbia, Vancouver, British Columbia, Canada.
Department of Medical Genetics, The University of British Columbia, Vancouver, British Columbia, Canada.
BC Children's Hospital Research Institute, The University of British Columbia, Vancouver, British Columbia, Canada.

Nicole M Roslin (NM)

The Centre for Applied Genomics, Hospital for Sick Children Research Institute, University of Toronto, Toronto, Ontario, Canada.

Andrew D Paterson (AD)

The Centre for Applied Genomics, Hospital for Sick Children Research Institute, University of Toronto, Toronto, Ontario, Canada.
Genetics and Genome Biology, Hospital for Sick Children, Toronto, Ontario, Canada.
Divisions of Epidemiology and Biostatistics, Dalla Lana School of Public Health, University of Toronto, Toronto, Ontario, Canada.

Christopher J Lyons (CJ)

BC Children's Hospital Research Institute, The University of British Columbia, Vancouver, British Columbia, Canada.
Department of Ophthalmology and Visual Sciences, The University of British Columbia, Vancouver, British Columbia, Canada.

Victor Pegado (V)

Department of Ophthalmology and Visual Sciences, The University of British Columbia, Vancouver, British Columbia, Canada.

Phillip Richmond (P)

Centre for Molecular Medicine and Therapeutics, The University of British Columbia, Vancouver, British Columbia, Canada.
BC Children's Hospital Research Institute, The University of British Columbia, Vancouver, British Columbia, Canada.

Casper Shyr (C)

Centre for Molecular Medicine and Therapeutics, The University of British Columbia, Vancouver, British Columbia, Canada.
BC Children's Hospital Research Institute, The University of British Columbia, Vancouver, British Columbia, Canada.

Oriol Fornes (O)

Centre for Molecular Medicine and Therapeutics, The University of British Columbia, Vancouver, British Columbia, Canada.
BC Children's Hospital Research Institute, The University of British Columbia, Vancouver, British Columbia, Canada.

XiaoHua Han (X)

Centre for Molecular Medicine and Therapeutics, The University of British Columbia, Vancouver, British Columbia, Canada.

Michelle Higginson (M)

Centre for Molecular Medicine and Therapeutics, The University of British Columbia, Vancouver, British Columbia, Canada.

Colin J Ross (CJ)

Faculty of Pharmaceutical Sciences, The University of British Columbia, Vancouver, British Columbia, Canada.

Deborah Giaschi (D)

BC Children's Hospital Research Institute, The University of British Columbia, Vancouver, British Columbia, Canada.
Department of Ophthalmology and Visual Sciences, The University of British Columbia, Vancouver, British Columbia, Canada.

Cheryl Gregory-Evans (C)

Department of Ophthalmology and Visual Sciences, The University of British Columbia, Vancouver, British Columbia, Canada.

Millan S Patel (MS)

Department of Medical Genetics, The University of British Columbia, Vancouver, British Columbia, Canada wyeth@cmmt.ubc.ca mpatel@cw.bc.ca.
BC Children's Hospital Research Institute, The University of British Columbia, Vancouver, British Columbia, Canada.

Wyeth W Wasserman (WW)

Centre for Molecular Medicine and Therapeutics, The University of British Columbia, Vancouver, British Columbia, Canada wyeth@cmmt.ubc.ca mpatel@cw.bc.ca.
Department of Medical Genetics, The University of British Columbia, Vancouver, British Columbia, Canada.
BC Children's Hospital Research Institute, The University of British Columbia, Vancouver, British Columbia, Canada.

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Classifications MeSH