A non-lethal presentation of osteogenesis imperfecta type VIII due to homozygous mutation in


Journal

BMJ case reports
ISSN: 1757-790X
Titre abrégé: BMJ Case Rep
Pays: England
ID NLM: 101526291

Informations de publication

Date de publication:
24 Oct 2024
Historique:
medline: 26 10 2024
pubmed: 26 10 2024
entrez: 25 10 2024
Statut: epublish

Résumé

A female toddler presented with short stature and hypermobility of limbs. She had sustained five long bone fractures following minor trauma since early infancy. Skeletal survey was consistent with osteogenesis imperfecta. This was genetically proven on clinical exome analysis, which revealed a pathogenic homozygous autosomal recessive

Identifiants

pubmed: 39455078
pii: 17/10/e260133
doi: 10.1136/bcr-2024-260133
pii:
doi:

Substances chimiques

P3H1 protein, human EC 1.14.11.7
Pamidronate OYY3447OMC
Cyclophilins EC 5.2.1.-
Bone Density Conservation Agents 0
Codon, Nonsense 0
Membrane Glycoproteins 0
Proteoglycans 0
Prolyl Hydroxylases EC 1.14.11.-

Types de publication

Case Reports Journal Article

Langues

eng

Sous-ensembles de citation

IM

Informations de copyright

© BMJ Publishing Group Limited 2024. No commercial re-use. See rights and permissions. Published by BMJ.

Déclaration de conflit d'intérêts

Competing interests: None declared.

Auteurs

Savita Khadse (S)

Pediatrics, Lokmanya Tilak Municipal General Hospital and Lokmanya Tilak Municipal Medical College, Mumbai, Maharashtra, India.

Prakruthi Shankaramurthy (P)

Pediatrics, Lokmanya Tilak Municipal General Hospital and Lokmanya Tilak Municipal Medical College, Mumbai, Maharashtra, India.

Nikhil Shah (N)

Pediatrics, Lokmanya Tilak Municipal General Hospital and Lokmanya Tilak Municipal Medical College, Mumbai, Maharashtra, India nikhilshah1507@gmail.com.
Division of Pediatric Endocrinology, Department of Pediatrics, Surya Childrens Hospital, Mumbai, Maharashtra, India.

Radha Ghildiyal (R)

Pediatrics, Lokmanya Tilak Municipal General Hospital and Lokmanya Tilak Municipal Medical College, Mumbai, Maharashtra, India.

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Classifications MeSH