Clinical and biological features of PTPN2-deleted adult and pediatric T-cell acute lymphoblastic leukemia.


Journal

Blood advances
ISSN: 2473-9537
Titre abrégé: Blood Adv
Pays: United States
ID NLM: 101698425

Informations de publication

Date de publication:
09 07 2019
Historique:
received: 20 11 2018
accepted: 06 05 2019
entrez: 5 7 2019
pubmed: 5 7 2019
medline: 10 7 2020
Statut: ppublish

Résumé

Protein tyrosine phosphatase nonreceptor type 2 (PTPN2) is a phosphatase known to be a tumor suppressor gene in T-cell acute lymphoblastic leukemia (T-ALL). Because the full clinicobiologic characteristics of PTPN2 loss remain poorly reported, we aimed to provide a comprehensive analysis of PTPN2 deletions within a cohort of 430 patients, including 216 adults and 214 children treated according to the GRAALL03/05 (#NCT00222027 and #NCT00327678) and the FRALLE2000 protocols, respectively. We used multiplex ligation-dependent probe amplification to identify an 8% incidence of PTPN2 deletion, which was comparable in adult (9%) and pediatric (6%) populations. PTPN2 deletions were significantly associated with an αβ lineage and TLX1 deregulation. Analysis of the mutational genotype of adult T-ALL revealed a positive correlation between PTPN2 deletions and gain-of-function alterations in the IL7R/JAK-STAT signaling pathway as well as PHF6 and WT1 mutations. Of note, PTPN2 and PTEN (phosphatase and tensin homolog) deletions were mutually exclusive. Regarding treatment response, PTPN2-deleted T-ALLs were associated with a higher glucocorticoid response and a trend for improved survival in children, but not in adults, with a 5-year cumulative incidence of relapse of 8% for PTPN2-deleted pediatric cases vs 26% (

Identifiants

pubmed: 31270080
pii: bloodadvances.2018028993
doi: 10.1182/bloodadvances.2018028993
pmc: PMC6616254
doi:

Substances chimiques

Biomarkers, Tumor 0
IL7R protein, human 0
Interleukin-7 Receptor alpha Subunit 0
STAT Transcription Factors 0
Janus Kinases EC 2.7.10.2
PTPN2 protein, human EC 3.1.3.48
Protein Tyrosine Phosphatase, Non-Receptor Type 2 EC 3.1.3.48

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1981-1988

Informations de copyright

© 2019 by The American Society of Hematology.

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Auteurs

Marion Alcantara (M)

Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades, Institut National de Recherche Médicale U1151, Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Hôpital Necker Enfants-Malades, Paris, France.

Mathieu Simonin (M)

Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades, Institut National de Recherche Médicale U1151, Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Hôpital Necker Enfants-Malades, Paris, France.
Department of Pediatric Hematology and Oncology, Assistance Publique-Hôpitaux de Paris, Groupe Hospitalier des Hôpitaux Universitaires Est Parisien, Armand Trousseau Hospital, Paris, France.
Sorbonne Universités, Université Pierre et Marie Curie Université Paris 06, Unité Mixte de Recherche S 938, Centre de Recherche Saint-Antoine, Groupe de Recherche (GRC) Clinique n°07, GRC Myéloproliférations aiguës et chroniques, Paris, France.

Ludovic Lhermitte (L)

Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades, Institut National de Recherche Médicale U1151, Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Hôpital Necker Enfants-Malades, Paris, France.

Aurore Touzart (A)

Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades, Institut National de Recherche Médicale U1151, Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Hôpital Necker Enfants-Malades, Paris, France.

Marie Emilie Dourthe (ME)

Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades, Institut National de Recherche Médicale U1151, Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Hôpital Necker Enfants-Malades, Paris, France.
Department of Pediatric Hematology and Immunology, Assistance Publique-Hôpitaux de Paris, Hôpital Universitaire Robert-Debré, Paris, France.

Mehdi Latiri (M)

Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades, Institut National de Recherche Médicale U1151, Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Hôpital Necker Enfants-Malades, Paris, France.

Nathalie Grardel (N)

Laboratory of Hematology, Centre Hospitalier Régional Universitaire de Lille, Lille, France.

Jean Michel Cayuela (JM)

Laboratory of Hematology, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.

Yves Chalandon (Y)

Swiss Group for Clinical Cancer Research, Bern, Hôpital Universitaire, Geneva, Switzerland.

Carlos Graux (C)

Université Catholique de Louvain, Centre Hospitalier Universitaire, Namur, Yvoir, Belgium.

Hervé Dombret (H)

Adolescent and Young Adult Hematology Unit, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France; and.

Norbert Ifrah (N)

Centre Hospitalier Universitaire d'Angers, Angers, France.

Arnaud Petit (A)

Department of Pediatric Hematology and Oncology, Assistance Publique-Hôpitaux de Paris, Groupe Hospitalier des Hôpitaux Universitaires Est Parisien, Armand Trousseau Hospital, Paris, France.
Sorbonne Universités, Université Pierre et Marie Curie Université Paris 06, Unité Mixte de Recherche S 938, Centre de Recherche Saint-Antoine, Groupe de Recherche (GRC) Clinique n°07, GRC Myéloproliférations aiguës et chroniques, Paris, France.

Elizabeth Macintyre (E)

Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades, Institut National de Recherche Médicale U1151, Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Hôpital Necker Enfants-Malades, Paris, France.

André Baruchel (A)

Department of Pediatric Hematology and Immunology, Assistance Publique-Hôpitaux de Paris, Hôpital Universitaire Robert-Debré, Paris, France.

Nicolas Boissel (N)

Adolescent and Young Adult Hematology Unit, Saint-Louis Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France; and.

Vahid Asnafi (V)

Université Paris Descartes Sorbonne Cité, Institut Necker-Enfants Malades, Institut National de Recherche Médicale U1151, Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Hôpital Necker Enfants-Malades, Paris, France.

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Classifications MeSH