Biallelic structural variants in three patients with ERCC8-related Cockayne syndrome and a potential pitfall of copy number variation analysis.


Journal

Scientific reports
ISSN: 2045-2322
Titre abrégé: Sci Rep
Pays: England
ID NLM: 101563288

Informations de publication

Date de publication:
26 08 2024
Historique:
received: 31 01 2024
accepted: 21 08 2024
medline: 27 8 2024
pubmed: 27 8 2024
entrez: 26 8 2024
Statut: epublish

Résumé

Cockayne syndrome (CS) is a rare autosomal recessive disorder caused by mutations in ERCC8 or ERCC6. Most pathogenic variants in ERCC8 are single nucleotide substitutions. Structural variants (SVs) have been reported in patients with ERCC8-related CS. However, comprehensive molecular detection, including SVs of ERCC8, in CS patients remains problematic. Herein, we present three Japanese patients with ERCC8-related CS in whom causative SVs were identified using whole-exome-based copy number variation (CNV) detection tools. One patient showed compound heterozygosity for a 259-kb deletion and a deletion of exon 4 which has previously been reported as an Asia-specific variant. The other two patients were homozygous for the same exon 4 deletion. The exon 4 deletion was detected only by the ExomeDepth software. Intrigued by the discrepancy in the detection capability of various tools for the SVs, we evaluated the analytic performance of four whole-exome-based CNV detection tools using an exome data set from 337 healthy individuals. A total of 1,278,141 exons were predicted as being affected by the 4 CNV tools. Interestingly 95.1% of these affected exons were detected by one tool alone. Thus, we expect that the use of multiple tools may improve the detection rate of SVs from aligned exome data.

Identifiants

pubmed: 39187681
doi: 10.1038/s41598-024-70831-7
pii: 10.1038/s41598-024-70831-7
doi:

Substances chimiques

ERCC8 protein, human 0
DNA Repair Enzymes EC 6.5.1.-
Transcription Factors 0

Types de publication

Journal Article Case Reports

Langues

eng

Sous-ensembles de citation

IM

Pagination

19741

Subventions

Organisme : Japan Society for the Promotion of Science
ID : 20K08236
Organisme : Japan Society for the Promotion of Science
ID : 20H03646
Organisme : Japan Agency for Medical Research and Development
ID : JP23ek0109549

Informations de copyright

© 2024. The Author(s).

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Auteurs

Daisuke Watanabe (D)

Center for Medical Genetics, Keio University School of Medicine, 35 Shinanomachi, Shinjuku, Tokyo, 160-8582, Japan.
Department of Pediatrics, Yamanashi University, Yamanashi, Japan.

Nobuhiko Okamoto (N)

Department of Medical Genetics, Osaka Women's and Children's Hospital, Osaka, Japan.

Yuichi Kobayashi (Y)

Professional Development Center, Tokyo Medical and Dental University (TMDU), Tokyo, Japan.

Hisato Suzuki (H)

Center for Medical Genetics, Keio University School of Medicine, 35 Shinanomachi, Shinjuku, Tokyo, 160-8582, Japan.
Department of Clinical Medicine, Institute of Medicine, University of Tsukuba, Ibaraki, Japan.

Mitsuhiro Kato (M)

Department of Pediatrics, Showa University School of Medicine, Tokyo, Japan.
Epilepsy Medical Center, Showa University Hospital, Tokyo, Japan.

Shinji Saitoh (S)

Department of Pediatrics and Neonatology, Nagoya City University Graduate School of Medical Sciences, Nagoya, Japan.

Yonehiro Kanemura (Y)

Department of Biomedical Research and Innovation, Institute for Clinical Research, NHO Osaka National Hospital, Osaka, Japan.
Department of Neurosurgery, NHO Osaka National Hospital, Osaka, Japan.

Toshiki Takenouchi (T)

Department of Pediatrics, Keio University School of Medicine, Tokyo, Japan.

Mamiko Yamada (M)

Center for Medical Genetics, Keio University School of Medicine, 35 Shinanomachi, Shinjuku, Tokyo, 160-8582, Japan.

Daisuke Nakato (D)

Center for Medical Genetics, Keio University School of Medicine, 35 Shinanomachi, Shinjuku, Tokyo, 160-8582, Japan.

Masayuki Sato (M)

Center for Medical Genetics, Keio University School of Medicine, 35 Shinanomachi, Shinjuku, Tokyo, 160-8582, Japan.

Tatsuhiko Tsunoda (T)

Laboratory for Medical Science Mathematics, Department of Biological Sciences, School of Science, The University of Tokyo, Tokyo, Japan.
Laboratory for Medical Science Mathematics, RIKEN Center for Integrative Medical Sciences, Yokohama, Japan.

Kenjiro Kosaki (K)

Center for Medical Genetics, Keio University School of Medicine, 35 Shinanomachi, Shinjuku, Tokyo, 160-8582, Japan.

Fuyuki Miya (F)

Center for Medical Genetics, Keio University School of Medicine, 35 Shinanomachi, Shinjuku, Tokyo, 160-8582, Japan. fmiya@keio.jp.
Innovative Human Resource Development Division, Institute of Education, Tokyo Medical and Dental University (TMDU), Tokyo, Japan. fmiya@keio.jp.

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