Novel familial IQSEC2 pathogenic sequence variant associated with neurodevelopmental disorders and epilepsy.


Journal

Neurogenetics
ISSN: 1364-6753
Titre abrégé: Neurogenetics
Pays: United States
ID NLM: 9709714

Informations de publication

Date de publication:
10 2020
Historique:
received: 13 01 2020
accepted: 11 05 2020
pubmed: 22 6 2020
medline: 16 6 2021
entrez: 22 6 2020
Statut: ppublish

Résumé

Pathogenic sequence variants in the IQ motif- and Sec7 domain-containing protein 2 (IQSEC2) gene have been confirmed as causative in the aetiopathogenesis of neurodevelopmental disorders (intellectual disability, autism) and epilepsy. We report on a case of a family with three sons; two of them manifest delayed psychomotor development and epilepsy. Initially proband A was examined using a multistep molecular diagnostics algorithm, including karyotype and array-comparative genomic hybridization analysis, both with negative results. Therefore, probands A and B and their unaffected parents were enrolled for an analysis using targeted "next-generation" sequencing (NGS) with a gene panel ClearSeq Inherited Disease

Identifiants

pubmed: 32564198
doi: 10.1007/s10048-020-00616-3
pii: 10.1007/s10048-020-00616-3
doi:

Substances chimiques

Guanine Nucleotide Exchange Factors 0
IQSEC2 protein, human 0

Types de publication

Case Reports Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

269-278

Auteurs

Marketa Wayhelova (M)

Department of Experimental Biology, Faculty of Science, Masaryk University, Brno, Czech Republic.
Department of Medical Genetics, University Hospital Brno, Brno, Czech Republic.

Michal Ryzí (M)

Clinic of Children's Neurology, University Hospital Brno, Brno, Czech Republic.

Jan Oppelt (J)

CEITEC-Central European Institute of Technology, Masaryk University, Brno, Czech Republic.

Eva Hladilkova (E)

Department of Medical Genetics, University Hospital Brno, Brno, Czech Republic.

Vladimira Vallova (V)

Department of Experimental Biology, Faculty of Science, Masaryk University, Brno, Czech Republic.
Department of Medical Genetics, University Hospital Brno, Brno, Czech Republic.

Lenka Krskova (L)

Department of Pathology and Molecular Medicine, 2nd Faculty of Medicine, Charles University in Prague and Motol University Hospital, Prague, Czech Republic.

Marcela Vilemova (M)

Department of Medical Genetics, University Hospital Brno, Brno, Czech Republic.

Hana Polackova (H)

Department of Experimental Biology, Faculty of Science, Masaryk University, Brno, Czech Republic.

Renata Gaillyova (R)

Department of Medical Genetics, University Hospital Brno, Brno, Czech Republic.

Petr Kuglik (P)

Department of Experimental Biology, Faculty of Science, Masaryk University, Brno, Czech Republic. kugl@sci.muni.cz.
Department of Medical Genetics, University Hospital Brno, Brno, Czech Republic. kugl@sci.muni.cz.

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Classifications MeSH