Patient-Derived Xenografts and Matched Cell Lines Identify Pharmacogenomic Vulnerabilities in Colorectal Cancer.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
15 10 2019
Historique:
received: 20 10 2018
revised: 13 06 2019
accepted: 29 07 2019
pubmed: 4 8 2019
medline: 22 9 2020
entrez: 4 8 2019
Statut: ppublish

Résumé

Patient-derived xenograft (PDX) models accurately recapitulate the tumor of origin in terms of histopathology, genomic landscape, and therapeutic response, but some limitations due to costs associated with their maintenance and restricted amenability for large-scale screenings still exist. To overcome these issues, we established a platform of 2D cell lines (xeno-cell lines, XL), derived from PDXs of colorectal cancer with matched patient germline gDNA available. Whole-exome and transcriptome sequencing analyses were performed. Biomarkers of response and resistance to anti-HER therapy were annotated. Dependency on the XLs recapitulated the entire spectrum of colorectal cancer transcriptional subtypes. Exome and RNA-seq analyses delineated several molecular biomarkers of response and resistance to EGFR and HER2 blockade. Genotype-driven responses observed The XL platform represents a preclinical tool for functional gene validation and proof-of-concept studies to identify novel druggable vulnerabilities in colorectal cancer.

Identifiants

pubmed: 31375513
pii: 1078-0432.CCR-18-3440
doi: 10.1158/1078-0432.CCR-18-3440
pmc: PMC7611232
mid: EMS128728
doi:

Substances chimiques

Biomarkers, Tumor 0
Lapatinib 0VUA21238F
WRN protein, human EC 3.6.4.12
Werner Syndrome Helicase EC 3.6.4.12
Trastuzumab P188ANX8CK

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

6243-6259

Subventions

Organisme : Wellcome Trust
Pays : United Kingdom
Organisme : European Research Council
ID : 724748
Pays : International
Organisme : Wellcome Trust
ID : 206194
Pays : United Kingdom

Informations de copyright

©2019 American Association for Cancer Research.

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Auteurs

Luca Lazzari (L)

Department of Oncology, University of Torino, Candiolo, Torino, Italy.

Giorgio Corti (G)

Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Gabriele Picco (G)

Wellcome Sanger Institute, Cambridge, United Kingdom.

Claudio Isella (C)

Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Monica Montone (M)

Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Pamela Arcella (P)

Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Erika Durinikova (E)

Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Eugenia R Zanella (ER)

Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Luca Novara (L)

Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Fabiane Barbosa (F)

Department of Interventional Radiology, Ospedale Niguarda Ca' Granda, Milan, Italy.

Andrea Cassingena (A)

Niguarda Cancer Center, Grande Ospedale Metropolitano Niguarda, Milan, Italy.

Carlotta Cancelliere (C)

Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Enzo Medico (E)

Department of Oncology, University of Torino, Candiolo, Torino, Italy.
Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Andrea Sartore-Bianchi (A)

Niguarda Cancer Center, Grande Ospedale Metropolitano Niguarda, Milan, Italy.
Department of Oncology and Hemato-Oncology, Università degli Studi di Milano, Milan, Italy.

Salvatore Siena (S)

Niguarda Cancer Center, Grande Ospedale Metropolitano Niguarda, Milan, Italy.
Department of Oncology and Hemato-Oncology, Università degli Studi di Milano, Milan, Italy.

Mathew J Garnett (MJ)

Wellcome Sanger Institute, Cambridge, United Kingdom.

Andrea Bertotti (A)

Department of Oncology, University of Torino, Candiolo, Torino, Italy.
Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Livio Trusolino (L)

Department of Oncology, University of Torino, Candiolo, Torino, Italy.
Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Federica Di Nicolantonio (F)

Department of Oncology, University of Torino, Candiolo, Torino, Italy.
Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Michael Linnebacher (M)

Department of General Surgery, Molecular Oncology and Immunotherapy, University of Rostock, Rostock, Germany.

Alberto Bardelli (A)

Department of Oncology, University of Torino, Candiolo, Torino, Italy.
Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

Sabrina Arena (S)

Department of Oncology, University of Torino, Candiolo, Torino, Italy. sabrina.arena@unito.it.
Candiolo Cancer Institute, FPO - IRCCS, Candiolo, Torino, Italy.

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